STAT5 and CD4+ T Cell Immunity [version 1; referees: 4 approved] by David L. Owen, Michael A. Farrar

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Cytotoxic CD4 T cells in the mucosa and in cancer by Hrishi Venkatesh, Hrishi Venkatesh, Sean I. Tracy, Sean I. Tracy, Michael A. Farrar, Michael A. Farrar

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Circulating neurofilaments to track dorsal root ganglion toxicity risks with AAV-mediated gene therapy by Michelle A. Farrar, Ewout Groen, Christiano Alves

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Biomarkers and the Development of a Personalized Medicine Approach in Spinal Muscular Atrophy by Didu S. T. Kariyawasam, Didu S. T. Kariyawasam, Arlene D'Silva, Cindy Lin, Monique M. Ryan, Michelle A. Farrar, Michelle A. Farrar

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An OGT-STAT5 Axis in Regulatory T Cells Controls Energy and Iron Metabolism by Zengdi Zhang, Oscar C. Salgado, Bing Liu, Zahra Moazzami, Zahra Moazzami, Kristin A. Hogquist, Kristin A. Hogquist, Michael A. Farrar, Michael A. Farrar, Hai-Bin Ruan, Hai-Bin Ruan

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Identification of Novel CSF-Derived miRNAs in Treated Paediatric Onset Spinal Muscular Atrophy: An Exploratory Study by Arlene M. D’Silva, Didu Kariyawasam, Pooja Venkat, Chelsea Mayoh, Michelle A. Farrar

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Collectin-11 (CL-11) Is a Major Sentinel at Epithelial Surfaces and Key Pattern Recognition Molecule in Complement-Mediated Ischaemic Injury by Christopher L. Nauser, Mark C. Howard, Giorgia Fanelli, Conrad A. Farrar, Steven Sacks

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Newborn screening for Duchenne muscular dystrophy: the perspectives of stakeholdersResearch in context by Charli Ji, Didu S. Kariyawasam, Hugo Sampaio, Michelle Lorentzos, Kristi J. Jones, Michelle A. Farrar

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Modelling the Cost-Effectiveness and Budget Impact of a Newborn Screening Program for Spinal Muscular Atrophy and Severe Combined Immunodeficiency by Sophy T. F. Shih, Elena Keller, Veronica Wiley, Michelle A. Farrar, Melanie Wong, Georgina M. Chambers

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Economic Evaluation of Newborn Screening for Severe Combined Immunodeficiency by Sophy T. F. Shih, Elena Keller, Veronica Wiley, Melanie Wong, Michelle A. Farrar, Georgina M. Chambers

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“The usual challenges of work are all magnified”: Australian paediatric health professionals’ experiences during the COVID-19 pandemic by Farah Akram, Madeleine Pidcock, Diane Oake, Gary F. Sholler, Michelle A. Farrar, Nadine A. Kasparian

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Phenotypic and Functional Diversity in Regulatory T Cells by Louisa E. Sjaastad, David L. Owen, Sean I. Tracy, Sean I. Tracy, Michael A. Farrar

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Rationale for targeting complement in COVID‐19 by Anastasia Polycarpou, Mark Howard, Conrad A Farrar, Roseanna Greenlaw, Giorgia Fanelli, Russell Wallis, Linda S Klavinskis, Steven Sacks

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The involvement of rare disease patient organisations in therapeutic innovation across rare paediatric neurological conditions: a narrative review by Christina Q. Nguyen, Kristine Alba-Concepcion, Elizabeth E. Palmer, Jackie L. Scully, Nicole Millis, Michelle A. Farrar

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Gene therapy-based strategies for spinal muscular atrophy—an Asia-Pacific perspective by Michelle A. Farrar, Loudella Calotes-Castillo, Ranil De Silva, Peter Barclay, Lani Attwood, Julie Cini, Monica Ferrie, Didu S. Kariyawasam

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Single-cell analysis identifies dynamic gene expression networks that govern B cell development and transformation by Robin D. Lee, Sarah A. Munro, Todd P. Knutson, Rebecca S. LaRue, Lynn M. Heltemes-Harris, Michael A. Farrar

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Corrosion threshold data of metallic materials in various operating environment of offshore wind turbine parts (tower, foundation, and nacelle/gearbox) by J.I. Ahuir-Torres, S. Simandjuntak, N. Bausch, A. Farrar, S. Webb, A. Nash, B. Thomas, J. Muna, C. Jonsson, D. Matthew

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Health, wellbeing and lived experiences of adults with SMA: a scoping systematic review by Hamish W. Y. Wan, Kate A. Carey, Arlene D’Silva, Steve Vucic, Matthew C. Kiernan, Nadine A. Kasparian, Michelle A. Farrar

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Alfalfa Seed Decontamination in Salmonella Outbreak by Christopher J. Gill, William E. Keene, Janet C. Mohle-Boetani, Jeff A. Farrar, Patti L. Waller, Christine G. Hahn, Paul R. Cieslak

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Combination therapeutics of Nilotinib and radiation in acute lymphoblastic leukemia as an effective method against drug-resistance. by Kamran Kaveh, Yutaka Takahashi, Michael A Farrar, Guy Storme, Marcucci Guido, Jamie Piepenburg, Jackson Penning, Jasmine Foo, Kevin Z Leder, Susanta K Hui

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