Evaluation of cell-penetrating peptide delivery of antisense oligonucleotides for therapeutic efficacy in spinal muscular atrophy by Hammond, S, Abendroth, F, Gait, M, Wood, M

Identification of a Peptide for Systemic Brain Delivery of a Morpholino Oligonucleotide in Mouse Models of Spinal Muscular Atrophy by Shabanpoor, F, Hammond, S, Abendroth, F, Hazell, G, Wood, M, Gait, M

Combining multiomics and drug perturbation profiles to identify muscle-specific treatments for spinal muscular atrophy by Meijboom, KE, Volpato, V, Monzón-Sandoval, J, Hoolachan, JM, Hammond, SM, Abendroth, F, de Jong, OG, Hazell, G, Ahlskog, N, Wood, MJ, Webber, C, Bowerman, M

Interventions targeting glucocorticoid-Krüppel-like factor 15-branched-chain amino acid signaling improve disease phenotypes in spinal muscular atrophy mice by Walter, L, Deguise, M, Meijboom, K, Betts, C, Ahlskog, N, Van Westering, T, Hazell, g, McFall, E, Kordala, A, Hammond, S, Abendroth, F, Murray, L, Shorrock, H, Prosdocimo, D, Haldar, S, Jain, M, Gillingwater, T, Claus, P, Kothary, R, Wood, M, Bowerman, M