Reversal of life-threatening hepatopulmonary syndrome in Gaucher disease by imiglucerase enzyme replacement therapy by Amal El Beshlawy, Vagishwari Murugesan, Pramod Kumar Mistry, Khaled Eid

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Study of the effect of HFE gene mutations on iron overload in Egyptian thalassemia patients by Manal Michel Wilson, Hanan Al-Wakeel, Fadwa Said, Mona El-Ghamrawy, Mary Assaad, Amal El-Beshlawy

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Results From a 12-Month Open-Label Phase 1/2 Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease by Azza A. G. Tantawy MD, Amal El-Beshlawy MD, Iman Marzouk MD, Ashish Bavdekar DCH, DNB, Yulin Qin PhD, Björn Mellgard MD, PhD, Hadhami Ben Turkia MD

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Random Forest Clustering Identifies Three Subgroups of β-Thalassemia with Distinct Clinical Severity by Angela Vitrano, Khaled M. Musallam, Antonella Meloni, Sebastiano Addario Pollina, Mehran Karimi, Amal El-Beshlawy, Mahmoud Hajipour, Vito Di Marco, Saqib Hussain Ansari, Aldo Filosa, Paolo Ricchi, Adriana Ceci, Shahina Daar, Efthymia Vlachaki, Sylvia Titi Singer, Zaki A. Naserullah, Alessia Pepe, Salvatore Scondotto, Gabriella Dardanoni, Fedele Bonifazi, Vijay G. Sankaran, Elliott Vichinsky, Ali T. Taher, Aurelio Maggio, International Working Group on Thalassemia (IWG-THAL)

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