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1
Carer burden in rare inherited diseases: a literature review and conceptual model by Kerry Sandilands, Angela Williams, Angela J. Rylands
Published 2022-12-01
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2
Craniosynostosis in Patients With X‐Linked Hypophosphatemia: A Review by Craig F Munns, Edward P Maguire, Angela Williams, Sue Wood, Andrew Biggin
Published 2023-05-01
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A patient-centred and multi-stakeholder co-designed observational prospective study protocol: Example of the adolescent experience of treatment for X-linked hypophosphataemia (XLH)... by Vrinda Saraff, Annemieke M Boot, Agnès Linglart, Oliver Semler, Pol Harvengt, Angela Williams, Karen M A Bailey, Fiona Glen, Elin Haf Davies, Sue Wood, Stephen Greentree, Angela J Rylands
Published 2024-01-01
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4
Safety and immunogenicity of 15-valent pneumococcal conjugate vaccine (PCV-15) compared to PCV-13 in healthy older adults by Helen L. Stacey, Jeffrey Rosen, James T. Peterson, Angela Williams-Diaz, Vanita Gakhar, Tina M. Sterling, Camilo J. Acosta, Katrina M. Nolan, Jianing Li, Alison Pedley, Patrice Benner, Chitrananda Abeygunawardana, Michael Kosinski, William J. Smith, Hari Pujar, Luwy K. Musey
Published 2019-03-01
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Benefit of burosumab in adults with X-linked hypophosphataemia (XLH) is maintained with long-term treatment by Karine Briot, Wei Sun, Rachel K Crowley, Maria Luisa Brandi, Stuart H Ralston, Peter Kamenický, Martine Cohen-Solal, Richard Keen, Angela Williams, Muhammad K Javaid, Robin H Lachmann, Annabel Nixon, Mark Nixon, Anne-Lise Lecoq, Sami Kolta, Jennifer S Walsh, Angela J Rylands
Published 2023-02-01
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Respiratory virus coinfections during the COVID-19 pandemic: epidemiologic analysis and clinical outcomes from the Phase 2/3 molnupiravir trial (MOVe-OUT) by Matthew G. Johnson, Julie M. Strizki, Erin Jensen, Jonathan Cohen, Christine Katlama, Roman Fishchuk, Alfredo Ponce-de-León, Nyda Fourie, Chien-Yu Cheng, Dorothy McCoy, Mary Vesnesky, Carmelle T. Norice, Ying Zhang, Angela Williams-Diaz, Michelle L. Brown, Patricia Carmelitano, Jay A. Grobler, Amanda Paschke, Carisa De Anda
Published 2024-03-01
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The International X-Linked Hypophosphatemia (XLH) Registry: first interim analysis of baseline demographic, genetic and clinical data by Gema Ariceta, Signe Sparre Beck-Nielsen, Annemieke M. Boot, Maria Luisa Brandi, Karine Briot, Carmen de Lucas Collantes, Francesco Emma, Sandro Giannini, Dieter Haffner, Richard Keen, Elena Levtchenko, Outi Mӓkitie, M. Zulf Mughal, Ola Nilsson, Dirk Schnabel, Liana Tripto-Shkolnik, Jonathan Liu, Angela Williams, Sue Wood, M. Carola Zillikens
Published 2023-09-01
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