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A favorable outcome in an infantile-onset Pompe patient with cross reactive immunological material (CRIM) negative disease with high dose enzyme replacement therapy and adjusted im... by Shiri Curelaru, Ankit K. Desai, Daniel Fink, Yoav Zehavi, Priya S. Kishnani, Ronen Spiegel
Published 2022-09-01
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Development of high sustained anti-drug antibody titers and corresponding clinical decline in a late-onset Pompe disease patient after 11+ years on enzyme replacement therapy by Katherine H. Kim, Ankit K. Desai, Erika R. Vucko, Tracy Boggs, Priya S. Kishnani, Barbara K. Burton
Published 2023-09-01
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Immunophenotype associated with high sustained antibody titers against enzyme replacement therapy in infantile-onset Pompe disease by Ankit K. Desai, P. Brian Smith, P. Brian Smith, John S. Yi, Amy S. Rosenberg, Trevor D. Burt, Trevor D. Burt, Priya S. Kishnani
Published 2024-01-01
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An updated management approach of Pompe disease patients with high-sustained anti-rhGAA IgG antibody titers: experience with bortezomib-based immunomodulation by Ankit K. Desai, Garima Shrivastava, Christina L. Grant, Raymond Y. Wang, Raymond Y. Wang, Trevor D. Burt, Trevor D. Burt, Priya S. Kishnani
Published 2024-03-01
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Optimizing treatment outcomes: immune tolerance induction in Pompe disease patients undergoing enzyme replacement therapy by Hui-An Chen, Hui-An Chen, Hui-An Chen, Rai-Hseng Hsu, Rai-Hseng Hsu, Rai-Hseng Hsu, Ching-Ya Fang, Ankit K. Desai, Ni-Chung Lee, Ni-Chung Lee, Ni-Chung Lee, Wuh-Liang Hwu, Wuh-Liang Hwu, Wuh-Liang Hwu, Fuu-Jen Tsai, Priya S. Kishnani, Yin-Hsiu Chien, Yin-Hsiu Chien, Yin-Hsiu Chien
Published 2024-04-01
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