Genome Editing for β-Hemoglobinopathies: Advances and Challenges by Giacomo Frati, Annarita Miccio

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Epigenetic Regulation of β-Globin Genes and the Potential to Treat Hemoglobinopathies through Epigenome Editing by Letizia Fontana, Zoe Alahouzou, Annarita Miccio, Panagiotis Antoniou

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Editorial: Mutation-Specific Gene Editing for Blood Disorders by Carsten Werner Lederer, Pietro Genovese, Annarita Miccio, Sjaak Philipsen

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The GATA1-HS2 enhancer allows persistent and position-independent expression of a β-globin transgene. by Annarita Miccio, Valentina Poletti, Francesca Tiboni, Claudia Rossi, Antonella Antonelli, Fulvio Mavilio, Giuliana Ferrari

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Transcription factor binding sites are genetic determinants of retroviral integration in the human genome. by Barbara Felice, Claudia Cattoglio, Davide Cittaro, Anna Testa, Annarita Miccio, Giuliana Ferrari, Lucilla Luzi, Alessandra Recchia, Fulvio Mavilio

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Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors. by Arianna Moiani, Annarita Miccio, Ermanno Rizzi, Marco Severgnini, Danilo Pellin, Julia Debora Suerth, Christopher Baum, Gianluca De Bellis, Fulvio Mavilio

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GATA Factor-Mediated Gene Regulation in Human Erythropoiesis by Oriana Romano, Luca Petiti, Tristan Felix, Vasco Meneghini, Michel Portafax, Chiara Antoniani, Mario Amendola, Silvio Bicciato, Clelia Peano, Annarita Miccio

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Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins by Giulia Pavani, Marine Laurent, Anna Fabiano, Erika Cantelli, Aboud Sakkal, Guillaume Corre, Peter J. Lenting, Jean-Paul Concordet, Magali Toueille, Annarita Miccio, Mario Amendola

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Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins by Giulia Pavani, Marine Laurent, Anna Fabiano, Erika Cantelli, Aboud Sakkal, Guillaume Corre, Peter J. Lenting, Jean-Paul Concordet, Magali Toueille, Annarita Miccio, Mario Amendola

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Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation by Alessia Cavazza, Annarita Miccio, Oriana Romano, Luca Petiti, Guidantonio Malagoli Tagliazucchi, Clelia Peano, Marco Severgnini, Ermanno Rizzi, Gianluca De Bellis, Silvio Bicciato, Fulvio Mavilio

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Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies by Mégane Brusson, Anne Chalumeau, Pierre Martinucci, Oriana Romano, Tristan Felix, Valentina Poletti, Samantha Scaramuzza, Sophie Ramadier, Cecile Masson, Giuliana Ferrari, Fulvio Mavilio, Marina Cavazzana, Mario Amendola, Annarita Miccio

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Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem Cells. by Valentina Poletti, Alessia Delli Carri, Guidantonio Malagoli Tagliazucchi, Andrea Faedo, Luca Petiti, Emilia Maria Cristina Mazza, Clelia Peano, Gianluca De Bellis, Silvio Bicciato, Annarita Miccio, Elena Cattaneo, Fulvio Mavilio

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Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression by Panagiotis Antoniou, Giulia Hardouin, Pierre Martinucci, Giacomo Frati, Tristan Felix, Anne Chalumeau, Letizia Fontana, Jeanne Martin, Cecile Masson, Megane Brusson, Giulia Maule, Marion Rosello, Carine Giovannangeli, Vincent Abramowski, Jean-Pierre de Villartay, Jean-Paul Concordet, Filippo Del Bene, Wassim El Nemer, Mario Amendola, Marina Cavazzana, Anna Cereseto, Oriana Romano, Annarita Miccio

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Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi by Alessia Cavazza, Ayal Hendel, Rasmus O. Bak, Paula Rio, Marc Güell, Duško Lainšček, Virginia Arechavala-Gomeza, Ling Peng, Fatma Zehra Hapil, Joshua Harvey, Francisco G. Ortega, Coral Gonzalez-Martinez, Carsten W. Lederer, Kasper Mikkelsen, Giedrius Gasiunas, Nechama Kalter, Manuel A.F.V. Gonçalves, Julie Petersen, Alejandro Garanto, Lluis Montoliu, Marcello Maresca, Stefan E. Seemann, Jan Gorodkin, Loubna Mazini, Rosario Sanchez, Juan R. Rodriguez-Madoz, Noelia Maldonado-Pérez, Torella Laura, Michael Schmueck-Henneresse, Cristina Maccalli, Julian Grünewald, Gloria Carmona, Neli Kachamakova-Trojanowska, Annarita Miccio, Francisco Martin, Giandomenico Turchiano, Toni Cathomen, Yonglun Luo, Shengdar Q. Tsai, Karim Benabdellah

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