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Allele-Specific Reduction of the Mutant Huntingtin Allele Using Transcription Activator-Like Effectors in Human Huntington's Disease Fibroblasts af Kyle D. Fink Ph.D, Peter Deng, Josh Gutierrez, Joseph S. Anderson, Audrey Torrest, Anvita Komarla, Stefanos Kalomoiris, Whitney Cary, Johnathon D. Anderson, William Gruenloh, Alexandra Duffy, Teresa Tempkin, Geralyn Annett, Vicki Wheelock, David J. Segal, Jan A. Nolta
Udgivet 2016-04-01
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