Gentherapie als Behandlungskonzept für erbliche Netzhauterkrankungen [Gene therapy as a treatment concept for inherited retinal diseases] by Bellingrath, J, Fischer, MD

Large animal model species in pluripotent stem cell therapy research and development for retinal diseases: a systematic review by Bellingrath, J, Li, KV, Aziz, K, Izzi, JM, Liu, YV, Singh, MS

In silico analysis of pathogenic CRB1 single nucleotide variants and their amenability to base editing as a potential lead for therapeutic intervention by Bellingrath, J-S, McClements, ME, Kaukonen, M, Fischer, MD, MacLaren, RE

Envisioning the development of a CRISPR-Cas mediated base editing strategy for a patient with a novel pathogenic CRB1 single nucleotide variant by Bellingrath, J-S, McClements, ME, Shanks, M, Clouston, P, Fischer, MD, MacLaren, RE

Laparoscopic liver resection in Caroli disease: a single-centre case series by Bellingrath, J, Schoening, W, Wabitsch, S, Brenzing, C, Arnold, A, Fehrenbach, U, Schmelzle, M, Pratschke, J

High symmetry of visual acuity and visual fields in RPGR-linked retinitis pigmentosa by Bellingrath, J-S, Ochakovski, GA, Seitz, IP, Kohl, S, Zrenner, E, Hanig, N, Prokisch, H, Weber, BH, Downes, SM, Ramsden, S, MacLaren, RE, Fischer, MD

Codon-optimized RPGR improves stability and efficacy of AAV8 gene therapy in two mouse models of X-linked retinitis pigmentosa by Fischer, MD, McClements, ME, Martinez-Fernandez de la Camara, C, Bellingrath, J-S, Dauletbekov, D, Ramsden, SC, Hickey, DG, Barnard, AR, MacLaren, RE