Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity by Lim, WF, Forouhan, M, Roberts, TC, Dabney, J, Ellerington, R, Speciale, AA, Manzano, R, Lieto, M, Sangha, G, Banerjee, S, Conceição, M, Cravo, L, Biscans, A, Roux, L, Pourshafie, N, Grunseich, C, Duguez, S, Khvorova, A, Pennuto, M, Cortes, CJ, La Spada, AR, Fischbeck, KH, Wood, MJA, Rinaldi, C