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A simplified purification protocol for recombinant adeno-associated virus vectors di Mark Potter, Bridget Lins, Mario Mietzsch, Regine Heilbronn, Kim Van Vliet, Paul Chipman, Mavis Agbandje-McKenna, Brian D Cleaver, Nathalie Clément, Barry J Byrne, Sergei Zolotukhin
Pubblicazione 2014-01-01
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Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation di Manuela Corti, Barry J. Byrne, Dominic J. Gessler, Grace Thompson, Samantha Norman, Jenna Lammers, Kirsten E. Coleman, Cristina Liberati, Melissa E. Elder, Maria L. Escolar, Ibrahim S. Tuna, Clementina Mesaros, Gary I. Kleiner, Deborah S. Barbouth, Heather L. Gray-Edwards, Nathalie Clement, Brian D. Cleaver, Guangping Gao
Pubblicazione 2023-09-01
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