Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: a national French retrospective study by Cécile Freihuber, Bahia Dahmani-Rabehi, Anaïs Brassier, Pierre Broué, Claude Cances, Brigitte Chabrol, Didier Eyer, François Labarthe, Philippe Latour, Thierry Levade, Samia Pichard, Caroline Sevin, Marie T. Vanier, Bénédicte Héron

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Impact of severe polyhandicap cared for at home on French informal caregivers’ burden: a cross-sectional study by Alexandra Afenjar, Stéphanie Valence, Pascal Auquier, Marie-Christine Rousseau, Karine Baumstarck, Maria Valkov, Agnés Felce, Catherine Brisse, Sherezad Khaldi-Cherif, Anderson Loundou, Tanguy Leroy, Souhali Haddadou, Cécile Freihuber, Julie Bonheur, Marie-Christine Nougues, Laurent Luciani, Jean-Pierre Nouet, Catherine Coiffier, Philippe Sellier, Sophie Mathieu, Moustafa Ardati, Delphine Héron, Diana Rodriguez, Diana Doummar, Marie-Laure Moutard, Daniel Willocq, Stéphane Pietra, Stéphane Lenormand, Elizabeth Grimont

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