Dose-response evaluation of intravenous gene therapy in a symptomatic mouse model of metachromatic leukodystrophy by Emilie Audouard, Nicolas Khefif, Charlotte Mansat, Océane Nelcha, Elena-Gaia Banchi, Camille Lupiet, Dominique Farabos, Antonin Lamaziere, Caroline Sevin, Françoise Piguet

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