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Preclinical assessment of splicing modulation therapy for ABCA4 variant c.768G>T in Stargardt disease de réir Dyah W. Karjosukarso, Femke Bukkems, Lonneke Duijkers, Tomasz Z. Tomkiewicz, Julia Kiefmann, Andrei Sarlea, Sander Bervoets, Irene Vázquez-Domínguez, Laurie L. Molday, Robert S. Molday, Mihai G. Netea, Carel B. Hoyng, Alejandro Garanto, Rob W. J. Collin
Foilsithe / Cruthaithe 2025-01-01
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