Cerebrospinal Fluid Proteomic Changes after Nusinersen in Patients with Spinal Muscular Atrophy by Marie Beaudin, Tahereh Kamali, Whitney Tang, Katharine A. Hagerman, Sally Dunaway Young, Lisa Ghiglieri, Dana M. Parker, Benoit Lehallier, Carolina Tesi-Rocha, Jacinda B. Sampson, Tina Duong, John W. Day

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Assessing the Assisted Six-Minute Cycling Test as a Measure of Endurance in Non-Ambulatory Patients with Spinal Muscular Atrophy (SMA) by Whitney J. Tang, Bo Gu, Samuel Montalvo, Sally Dunaway Young, Dana M. Parker, Constance de Monts, Paxton Ataide, Noirin Ni Ghiollagain, Matthew T. Wheeler, Carolina Tesi Rocha, Jeffrey W. Christle, Zihuai He, John W. Day, Tina Duong

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Medical management of muscle weakness in Duchenne muscular dystrophy. by Sarah R Rivera, Sumit K Jhamb, Hoda Z Abdel-Hamid, Gyula Acsadi, John Brandsema, Emma Ciafaloni, Basil T Darras, Susan T Iannaccone, Chamindra G Konersman, Nancy L Kuntz, Craig M McDonald, Julie A Parsons, Carolina Tesi Rocha, Craig M Zaidman, Russell J Butterfield, Anne M Connolly, Katherine D Mathews

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