An empirical tool for estimating the share of unmet need due to healthcare inefficiencies, suboptimal access, and lack of effective technologies by Devin Incerti, John Browne, Caroline Huber, Christine L. Baker, Geoff Makinson, Amir Goren, Richard Willke, Warren Stevens

Get full text

Clinical and economic burden of achondroplasia in the United States: results from a retrospective, observational study by Nadia Merchant, Jose Alvir, Paulette Negron Ericksen, Jane Loftus, Jose Francisco Cara, Alison Slade, Michael P. Wajnrajch, Christine L. Baker

Get full text

Key measurement concepts and appropriate clinical outcome assessments in pediatric achondroplasia clinical trials by Natalie V. J. Aldhouse, Helen Kitchen, Chloe Johnson, Chris Marshall, Hannah Pegram, Sheryl Pease, Sam Collins, Christine L. Baker, Katherine Beaverson, Chandler Crews, Jill Massey, Kathleen W. Wyrwich

Get full text