Showing 1 - 2 results of 2 for search 'Claudia Perna', query time: 0.02s
Refine Results
-
1
Genome editing without nucleases confers proliferative advantage to edited hepatocytes and corrects Wilson disease by Agnese Padula, Michele Spinelli, Edoardo Nusco, Xabier Bujanda Cundin, Filomena Capolongo, Severo Campione, Claudia Perna, Amy Bastille, Megan Ericson, Chih-Chieh Wang, Shengwen Zhang, Angela Amoresano, Mariana Nacht, Pasquale Piccolo
Published 2023-11-01
Article -
2
Full-length ATP7B reconstituted through protein trans-splicing corrects Wilson disease in mice by Agnese Padula, Raffaella Petruzzelli, Sasha A. Philbert, Stephanie J. Church, Federica Esposito, Severo Campione, Marcello Monti, Filomena Capolongo, Claudia Perna, Edoardo Nusco, Hartmut H. Schmidt, Alberto Auricchio, Garth J.S. Cooper, Roman Polishchuk, Pasquale Piccolo
Published 2022-09-01
Article