Infantile spinal muscular atrophy: Therapeutic (R)evolution by Daron, A, Delstanche, S, Dangouloff, T, Servais, L

Sitting in patients with spinal muscular atrophy type 1 treated with nusinersen by Aragon-Gawinska, K, Daron, A, Ulinici, A, Vanden Brande, L, Seferian, A, Gidaro, T, Scoto, M, Deconinck, N, Servais, L, SMA-Registry Study Group

Versatile silicon-waveguide supercontinuum for coherent mid-infrared spectroscopy by Nima Nader, Daniel L. Maser, Flavio C. Cruz, Abijith Kowligy, Henry Timmers, Jeff Chiles, Connor Fredrick, Daron A. Westly, Sae Woo Nam, Richard P. Mirin, Jeffrey M. Shainline, Scott Diddams

Get full text

Nusinersen in patients older than 7 months with spinal muscular atrophy type 1: A cohort study by Aragon-Gawinska, K, Seferian, AM, Daron, A, Gargaun, E, Vuillerot, C, Cances, C, Ropars, J, Chouchane, M, Cuppen, I, Hughes, I, Illingworth, M, Marini-Bettolo, C, Rambaud, J, Taytard, J, Annoussamy, M, Scoto, M, Gidaro, T, Servais, LJP

Prospective and longitudinal natural history study of patients with Type 2 and 3 spinal muscular atrophy: Baseline data NatHis-SMA study by Chabanon, A, Seferian, AM, Daron, A, Péréon, Y, Cances, C, Vuillerot, C, De Waele, L, Cuisset, J-M, Laugel, V, Schara, U, Gidaro, T, Gilabert, S, Hogrel, J-Y, Baudin, P-Y, Carlier, P, Fournier, E, Lowes, LP, Hellbach, N, Seabrook, T, Toledano, E, Annoussamy, M, Servais, L

X-linked myotubular myopathy: A prospective international natural history study by Servais, L, Annoussamy, M, Lilien, C, Gidaro, T, Gargaun, E, Chê, V, Schara, U, Gangfuß, A, D'Amico, A, Dowling, JJ, Darras, BT, Daron, A, Hernandez, A, de Lattre, C, Arnal, J-M, Mayer, M, Cuisset, J-M, Vuillerot, C, Fontaine, S, Bellance, R, Biancalana, V, Buj-Bello, A, Hogrel, J-Y, Landy, H