Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease by Tyler B. Johnson, Tyler B. Johnson, Jon J. Brudvig, Jon J. Brudvig, Shibi Likhite, Melissa A. Pratt, Katherine A. White, Jacob T. Cain, Jacob T. Cain, Clarissa D. Booth, Derek J. Timm, Samantha S. Davis, Brandon Meyerink, Ricardo Pineda, Cassandra Dennys-Rivers, Brian K. Kaspar, Kathrin Meyer, Jill M. Weimer, Jill M. Weimer, Jill M. Weimer

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