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P1735: IMPROVEMENTS IN PATIENT-REPORTED OUTCOMES IN MITAPIVAT-TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL by K. H. Kuo, R. F. Grace, E. J. van Beers, W. Barcellini, A. Glenthøj, S. Holzhauer, P. Patel, V. Beynon, J. Li, E. Zagadailov, H. Al-Samkari
Published 2022-06-01
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