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Bioengineered Cystinotic Kidney Tubules Recapitulate a Nephropathic Phenotype by Elena Sendino Garví, Rosalinde Masereeuw, Manoe J. Janssen
Published 2022-01-01
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Evaluation of the efficacy of cystinosin supplementation through CTNS mRNA delivery in experimental models for cystinosis by Tjessa Bondue, Sante Princiero Berlingerio, Florian Siegerist, Elena Sendino-Garví, Maximilian Schindler, Hans Jacobus Baelde, Sara Cairoli, Bianca Maria Goffredo, Fanny Oliveira Arcolino, Jürgen Dieker, Manoe Jacoba Janssen, Nicole Endlich, Roland Brock, Rik Gijsbers, Lambertus van den Heuvel, Elena Levtchenko
Published 2023-11-01
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