Natural history of cognitive development in neuronopathic mucopolysaccharidosis type II (Hunter syndrome): Contribution of genotype to cognitive developmental course Autor Joo-Hyun Seo, Torayuki Okuyama, Elsa Shapiro, Yasuyuki Fukuhara, Motomichi Kosuga

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Association of somatic burden of disease with age and neuropsychological measures in attenuated mucopolysaccharidosis types I, II and VI Autor Alia Ahmed, Elsa Shapiro, Kyle Rudser, Alicia Kunin-Batson, Kelly King, Chester B. Whitley

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Analysis of the caregiver burden associated with Sanfilippo syndrome type B: panel recommendations based on qualitative and quantitative data Autor Elsa Shapiro, Charles Marques Lourenço, Neslihan Onenli Mungan, Nicole Muschol, Cara O’Neill, Suresh Vijayaraghavan

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Long-term cognitive and somatic outcomes of enzyme replacement therapy in untransplanted Hurler syndrome Autor Julie B. Eisengart, Jeanine Jarnes, Alia Ahmed, Igor Nestrasil, Richard Ziegler, Kathleen Delaney, Elsa Shapiro, Chester Whitley

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A longitudinal study of neurocognition and behavior in patients with Hurler-Scheie syndrome heterozygous for the L238Q mutation Autor Alia Ahmed, Li Ou, Kyle Rudser, Elsa Shapiro, Julie B. Eisengart, Kelly King, Agnes Chen, Patricia Dickson, Chester B. Whitley

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Recommendations on clinical trial design for treatment of Mucopolysaccharidosis Type III Autor Arunabha Ghosh, Elsa Shapiro, Stewart Rust, Kathleen Delaney, Samantha Parker, Adam J Shaywitz, Adelaida Morte, Gillian Bubb, Maureen Cleary, Tien Bo, Christine Lavery, Brian W Bigger, Simon A Jones

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