Givinostat for Becker muscular dystrophy: A randomized, placebo-controlled, double-blind study by Giacomo P. Comi, Giacomo P. Comi, Erik H. Niks, Erik H. Niks, Krista Vandenborne, Claudia M. Cinnante, Hermien E. Kan, Hermien E. Kan, Rebecca J. Willcocks, Daniele Velardo, Francesca Magri, Michela Ripolone, Jules J. van Benthem, Nienke M. van de Velde, Nienke M. van de Velde, Simone Nava, Laura Ambrosoli, Sara Cazzaniga, Paolo U. Bettica

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Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials by Craig M. McDonald, James Signorovitch, Eugenio Mercuri, Erik H. Niks, Brenda Wong, Mirko Fillbrunn, Gautam Sajeev, Erica Yim, Ibrahima Dieye, Debra Miller, Susan J. Ward, Nathalie Goemans

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Comparison of two corticosteroid regimens on brain volumetrics in patients with Duchenne muscular dystrophy by Sam Geuens, Jeroen Van Dessel, Rosanne Govaarts, Nadine A. Ikelaar, Onno C. Meijer, Hermien E. Kan, Erik H. Niks, Nathalie Goemans, Jurgen Lemiere, Nathalie Doorenweerd, Liesbeth De Waele

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Age-related longitudinal changes in metabolic energy expenditure during walking in boys with Duchenne muscular dystrophy. by Merel-Anne Brehm, Jiska C E Kempen, Anneke J van der Kooi, Imelda J M de Groot, Janneke C van den Bergen, Jan J G M Verschuuren, Erik H Niks, Jaap Harlaar

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Author Correction: Timing and localization of human dystrophin isoform expression provide insights into the cognitive phenotype of Duchenne muscular dystrophy by Nathalie Doorenweerd, Ahmed Mahfouz, Maaike van Putten, Rajaram Kaliyaperumal, Peter A. C. t’ Hoen, Jos G. M. Hendriksen, Annemieke M. Aartsma-Rus, Jan J. G. M. Verschuuren, Erik H. Niks, Marcel J. T. Reinders, Hermien E. Kan, Boudewijn P. F. Lelieveldt

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Preserved thenar muscles in non‐ambulant Duchenne muscular dystrophy patients by Karin J. Naarding, Kevin R. Keene, Aashley S.D. Sardjoe Mishre, Thom T.J. Veeger, Nienke M. van deVelde, Arina J. Prins, Jedrzej Burakiewicz, Jan J.G.M. Verschuuren, Menno van derHolst, Erik H. Niks, Hermien E. Kan

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Tracking disease progression non‐invasively in Duchenne and Becker muscular dystrophies by Pietro Spitali, Kristina Hettne, Roula Tsonaka, Mohammed Charrout, Janneke van denBergen, Zaïda Koeks, Hermien E. Kan, Melissa T. Hooijmans, Andreas Roos, Volker Straub, Francesco Muntoni, Cristina Al‐Khalili‐Szigyarto, Marleen J.A. Koel‐Simmelink, Charlotte E. Teunissen, Hanns Lochmüller, Erik H. Niks, Annemieke Aartsma‐Rus

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Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study by Francesco Muntoni, James Signorovitch, Gautam Sajeev, Nicolae Done, Zhiwen Yao, Nathalie Goemans, Craig McDonald, Eugenio Mercuri, Erik H. Niks, Brenda Wong, Krista Vandenborne, Volker Straub, Imelda J. M. de Groot, Cuixia Tian, Adnan Manzur, Ibrahima Dieye, Henry Lane, Susan J. Ward, Laurent Servais

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Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy by Vandana Ayyar Gupta, Jacqueline M. Pitchforth, Joana Domingos, Deborah Ridout, Mario Iodice, Catherine Rye, Mary Chesshyre, Amy Wolfe, Victoria Selby, Anna Mayhew, Elena S. Mazzone, Valeria Ricotti, Jean-Yves Hogrel, Erik H. Niks, Imelda de Groot, Laurent Servais, Volker Straub, Eugenio Mercuri, Adnan Y. Manzur, Francesco Muntoni

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Diffusion‐tensor magnetic resonance imaging captures increased skeletal muscle fibre diameters in Becker muscular dystrophy by Donnie Cameron, Tooba Abbassi‐Daloii, Laura G.M. Heezen, Nienke M. van deVelde, Zaïda Koeks, Thom T.J. Veeger, Melissa T. Hooijmans, Salma elAbdellaoui, Sjoerd G. vanDuinen, Jan J.G.M. Verschuuren, Maaike vanPutten, Annemieke Aartsma‐Rus, Vered Raz, Pietro Spitali, Erik H. Niks, Hermien E. Kan

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Determining minimal clinically important differences in the North Star Ambulatory Assessment (NSAA) for patients with Duchenne muscular dystrophy. by Vandana Ayyar Gupta, Jacqueline M Pitchforth, Joana Domingos, Deborah Ridout, Mario Iodice, Catherine Rye, Mary Chesshyre, Amy Wolfe, Victoria Selby, Anna Mayhew, Elena S Mazzone, Valeria Ricotti, Jean-Yves Hogrel, Erik H Niks, Imelda de Groot, Laurent Servais, Volker Straub, Eugenio Mercuri, Adnan Y Manzur, Francesco Muntoni, iMDEX Consortium and the U.K. NorthStar Clinical Network

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Prevalence of Bladder and Bowel Dysfunction in Duchenne Muscular Dystrophy Using the Childhood Bladder and Bowel Dysfunction Questionnaire by Judith M. Lionarons, Imelda J. M. de Groot, Johanna M. Fock, Sylvia Klinkenberg, Desiree M. J. Vrijens, Anita C. E. Vreugdenhil, Evita G. Medici-van den Herik, Inge Cuppen, Bregje Jaeger, Erik H. Niks, Rinske Hoogerhuis, Nicky Platte-van Attekum, Frans J. M. Feron, Catharina G. Faber, Jos G. M. Hendriksen, Johan S. H. Vles

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Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study. by Francesco Muntoni, James Signorovitch, Gautam Sajeev, Nicolae Done, Zhiwen Yao, Nathalie Goemans, Craig McDonald, Eugenio Mercuri, Erik H Niks, Brenda Wong, Krista Vandenborne, Volker Straub, Imelda J M de Groot, Cuixia Tian, Adnan Manzur, Ibrahima Dieye, Henry Lane, Susan J Ward, Laurent Servais, PRO-DMD-01 study investigators, Association Française contre les Myopathies, UK NorthStar Clinical Network, ImagingDMD investigators, cTAP

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