Dissection of splicing regulation at an endogenous locus by zinc-finger nuclease-mediated gene editing. by Sandra Cristea, Philip D Gregory, Fyodor D Urnov, Gregory J Cost

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Disruption of the BCL11A Erythroid Enhancer Reactivates Fetal Hemoglobin in Erythroid Cells of Patients with β-Thalassemia Major by Nikoletta Psatha, Andreas Reik, Susan Phelps, Yuanyue Zhou, Demetri Dalas, Evangelia Yannaki, Dana N. Levasseur, Fyodor D. Urnov, Michael C. Holmes, Thalia Papayannopoulou

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Piloting an integrated SARS-CoV-2 testing and data system for outbreak containment among college students: A prospective cohort study. by Laura Packel, Arthur Reingold, Lauren Hunter, Shelley Facente, Yi Li, Anna Harte, Guy Nicolette, Fyodor D Urnov, Michael Lu, Maya Petersen, IGI Testing Consortium

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Human Intestinal Tissue with Adult Stem Cell Properties Derived from Pluripotent Stem Cells by Ryan Forster, Kunitoshi Chiba, Lorian Schaeffer, Samuel G. Regalado, Christine S. Lai, Qing Gao, Samira Kiani, Henner F. Farin, Hans Clevers, Gregory J. Cost, Andy Chan, Edward J. Rebar, Fyodor D. Urnov, Philip D. Gregory, Lior Pachter, Rudolf Jaenisch, Dirk Hockemeyer

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Human Intestinal Tissue with Adult Stem Cell Properties Derived from Pluripotent Stem Cells by Ryan Forster, Kunitoshi Chiba, Lorian Schaeffer, Samuel G. Regalado, Christine S. Lai, Qing Gao, Samira Kiani, Henner F. Farin, Hans Clevers, Gregory J. Cost, Andy Chan, Edward J. Rebar, Fyodor D. Urnov, Philip D. Gregory, Lior Pachter, Rudolf Jaenisch, Dirk Hockemeyer

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LRRK2 mutations cause mitochondrial DNA damage in iPSC-derived neural cells from Parkinson's disease patients: Reversal by gene correction by Laurie H. Sanders, Josée Laganière, Oliver Cooper, Sally K. Mak, B. Joseph Vu, Y. Anne Huang, David E. Paschon, Malini Vangipuram, Ramya Sundararajan, Fyodor D. Urnov, J. William Langston, Philip D. Gregory, H. Steve Zhang, J. Timothy Greenamyre, Ole Isacson, Birgitt Schüle

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Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34+ Hematopoietic Stem and Progenitor Cells by Kai-Hsin Chang, Sarah E. Smith, Timothy Sullivan, Kai Chen, Qianhe Zhou, Jason A. West, Mei Liu, Yingchun Liu, Benjamin F. Vieira, Chao Sun, Vu P. Hong, Mingxuan Zhang, Xiao Yang, Andreas Reik, Fyodor D. Urnov, Edward J. Rebar, Michael C. Holmes, Olivier Danos, Haiyan Jiang, Siyuan Tan

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Global Regulatory DNA Potentiation by SMARCA4 Propagates to Selective Gene Expression Programs via Domain-Level Remodeling by John E. Lazar, Sandra Stehling-Sun, Vivek Nandakumar, Hao Wang, Daniel R. Chee, Nicholas P. Howard, Reyes Acosta, Douglass Dunn, Morgan Diegel, Fidencio Neri, Andres Castillo, Sean Ibarrientos, Kristen Lee, Ninnia Lescano, Ben Van Biber, Jemma Nelson, Jessica Halow, Richard Sandstrom, Daniel Bates, Fyodor D. Urnov, Alister P.W. Funnell, John A. Stamatoyannopoulos

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Robotic RNA extraction for SARS-CoV-2 surveillance using saliva samples by Jennifer R. Hamilton, Elizabeth C. Stahl, Connor A. Tsuchida, Enrique Lin-Shiao, C. Kimberly Tsui, Kathleen Pestal, Holly K. Gildea, Lea B. Witkowsky, Erica A. Moehle, Shana L. McDevitt, Matthew McElroy, Amanda Keller, Iman Sylvain, Ariana Hirsh, Alison Ciling, Alexander J. Ehrenberg, Bradley R. Ringeisen, Garth Huberty, Fyodor D. Urnov, Petros Giannikopoulos, Jennifer A. Doudna, IGI SARS-CoV-2 Consortium

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Robotic RNA extraction for SARS-CoV-2 surveillance using saliva samples. by Jennifer R Hamilton, Elizabeth C Stahl, Connor A Tsuchida, Enrique Lin-Shiao, C Kimberly Tsui, Kathleen Pestal, Holly K Gildea, Lea B Witkowsky, Erica A Moehle, Shana L McDevitt, Matthew McElroy, Amanda Keller, Iman Sylvain, Ariana Hirsh, Alison Ciling, Alexander J Ehrenberg, Bradley R Ringeisen, Garth Huberty, Fyodor D Urnov, Petros Giannikopoulos, Jennifer A Doudna, IGI SARS-CoV-2 Consortium

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LuNER: Multiplexed SARS-CoV-2 detection in clinical swab and wastewater samples. by Elizabeth C Stahl, Allan R Gopez, Connor A Tsuchida, Vinson B Fan, Erica A Moehle, Lea B Witkowsky, Jennifer R Hamilton, Enrique Lin-Shiao, Matthew McElroy, Shana L McDevitt, Alison Ciling, C Kimberly Tsui, Kathleen Pestal, Holly K Gildea, Amanda Keller, Iman A Sylvain, Clara Williams, Ariana Hirsh, Alexander J Ehrenberg, Rose Kantor, Matthew Metzger, Kara L Nelson, Fyodor D Urnov, Bradley R Ringeisen, Petros Giannikopoulos, Jennifer A Doudna, IGI Testing Consortium

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Evidence generation and reproducibility in cell and gene therapy research: A call to action by Mohamed Abou-el-Enein, Aris Angelis, Frederick R. Appelbaum, Nancy C. Andrews, Susan E. Bates, Arlene S. Bierman, Malcolm K. Brenner, Marina Cavazzana, Michael A. Caligiuri, Hans Clevers, Emer Cooke, George Q. Daley, Victor J. Dzau, Lee M. Ellis, Harvey V. Fineberg, Lawrence S.B. Goldstein, Stephen Gottschalk, Margaret A. Hamburg, Donald E. Ingber, Donald B. Kohn, Adrian R. Krainer, Marcela V. Maus, Peter Marks, Christine L. Mummery, Roderic I. Pettigrew, Joni L. Rutter, Sarah A. Teichmann, Andre Terzic, Fyodor D. Urnov, David A. Williams, Jedd D. Wolchok, Mark Lawler, Cameron J. Turtle, Gerhard Bauer, John P.A. Ioannidis

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Launching a saliva-based SARS-CoV-2 surveillance testing program on a university campus. by Alexander J Ehrenberg, Erica A Moehle, Cara E Brook, Andrew H Doudna Cate, Lea B Witkowsky, Rohan Sachdeva, Ariana Hirsh, Kerrie Barry, Jennifer R Hamilton, Enrique Lin-Shiao, Shana McDevitt, Luis Valentin-Alvarado, Kaitlyn N Letourneau, Lauren Hunter, Amanda Keller, Kathleen Pestal, Phillip A Frankino, Andrew Murley, Divya Nandakumar, Elizabeth C Stahl, Connor A Tsuchida, Holly K Gildea, Andrew G Murdock, Megan L Hochstrasser, Elizabeth O'Brien, Alison Ciling, Alexandra Tsitsiklis, Kurtresha Worden, Claire Dugast-Darzacq, Stephanie G Hays, Colin C Barber, Riley McGarrigle, Emily K Lam, David C Ensminger, Lucie Bardet, Carolyn Sherry, Anna Harte, Guy Nicolette, Petros Giannikopoulos, Dirk Hockemeyer, Maya Petersen, Fyodor D Urnov, Bradley R Ringeisen, Mike Boots, Jennifer A Doudna, IGI SARS-CoV-2 Testing Consortium

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