Long-term data with idebenone on respiratory function outcomes in patients with Duchenne muscular dystrophy Por Servais, L, Straathof, CSM, Schara, U, Klein, A, Leinonen, M, Hasham, S, Meier, T, De Waele, L, Gordish-Dressman, H, McDonald, CM, Mayer, OH, Voit, T, Mercuri, E, Buyse, GM

Towards regulatory endorsement of drug development tools to promote the application of model-informed drug development in Duchenne muscular dystrophy Por Conrado, DJ, Larkindale, J, Berg, A, Hill, M, Burton, J, Abrams, KR, Abresch, RT, Bronson, A, Chapman, D, Crowther, M, Duong, T, Gordish-Dressman, H, Harnisch, L, Henricson, E, Kim, S, McDonald, CM, Schmidt, S, Vong, C, Wang, X, Wong, BL, Yong, F, Romero, K, Duchenne Muscular Dystrophy Regulatory Science Consortium (D-RSC)