Yazar Araması Sonucu :: UTM Library Massive Scholar Tracking

1

Engineering exon-skipping vectors expressing U7 snRNA constructs for Duchenne muscular dystrophy gene therapy. Yazar: Goyenvalle, A, Davies, K

Baskı/Yayın Bilgisi 2011

Journal article

2

Challenges to oligonucleotides-based therapeutics for Duchenne muscular dystrophy. Yazar: Goyenvalle, A, Davies, K

Baskı/Yayın Bilgisi 2011

Journal article

3

Therapeutic approaches to muscular dystrophy. Yazar: Goyenvalle, A, Seto, J, Davies, K, Chamberlain, J

Baskı/Yayın Bilgisi 2011

Journal article

4

AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Babbs, A, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2010

Conference item

5

Upgrading U7snRNA To Complete Efficient Rescue of Dystrophin by Exon-Skipping in DMD Patients Yazar: Goyenvalle, A, Babbs, A, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2009

Conference item

6

AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Babbs, A, Wright, J, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2011

Conference item

7

Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy. Yazar: Goyenvalle, A, Babbs, A, van Ommen, G, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2009

Journal article

8

The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery. Yazar: Eckenfelder, A, Tordo, J, Babbs, A, Davies, K, Goyenvalle, A, Danos, O

Baskı/Yayın Bilgisi 2012

Journal article

9

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Wright, J, Babbs, A, Wilkins, V, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2012

Journal article

10

Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping. Yazar: Goyenvalle, A, Babbs, A, Powell, D, Kole, R, Fletcher, S, Wilton, S, Davies, K

Baskı/Yayın Bilgisi 2010

Journal article

11

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy. Yazar: Goyenvalle, A, Wright, J, Babbs, A, Wilkins, V, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2012

Journal article

12

Rescu of severely affected dystrophin/utrophin deficient mice by morpholino-oligomer mediated exon skipping Yazar: Goyenvalle, A, Babbs, A, Powell, D, Kole, R, Fletcher, S, Wilton, S, Davies, K

Baskı/Yayın Bilgisi 2010

Conference item

13

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping Yazar: Goyenvalle, A, Babbs, A, Wright, J, Wilkins, V, Powell, D, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2012

Journal article

14

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping. Yazar: Goyenvalle, A, Babbs, A, Wright, J, Wilkins, V, Powell, D, Garcia, L, Davies, K

Baskı/Yayın Bilgisi 2012

Conference item

15

AAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy Yazar: Le Hir, M, Goyenvalle, A, Peccate, C, Précigout, G, Davies, K, Voit, T, Garcia, L, Lorain, S

Baskı/Yayın Bilgisi 2013

Journal article

16

Tricyclo-DNA: A promising chemistry for the synthesis of antisense molecules for splice-switching approaches in DMD Yazar: Goyenvalle, A, Babbs, A, Avril, A, Griffiths, G, Dugovic, B, Davies, K, Leumann, C, Garcia, L

Baskı/Yayın Bilgisi 2012

Conference item

17

Diaphragm rescue alone prevents heart dysfunction in dystrophic mice. Yazar: Crisp, A, Yin, H, Goyenvalle, A, Betts, C, Moulton, H, Seow, Y, Babbs, A, Merritt, T, Saleh, A, Gait, M, Stuckey, D, Clarke, K, Davies, K, Wood, M

Baskı/Yayın Bilgisi 2011

Journal article

18

Delivery is key: lessons learnt from developing splice-switching antisense therapies Yazar: Godfrey, C, Desviat, L, Smedsrød, B, Piétri-Rouxel, F, Denti, M, Disterer, P, Lorain, S, Nogales-Gadea, G, Sardone, V, Anwar, R, El Andaloussi, S, Lehto, T, Khoo, B, Brolin, C, , v, Goyenvalle, A, Aartsma-Rus, A, Arechavala-Gomeza, V

Baskı/Yayın Bilgisi 2017

Journal article

19

Stakeholder cooperation to overcome challenges in orphan medicine development: the example of Duchenne muscular dystrophy Yazar: Straub, V, Balabanov, P, Bushby, K, Ensini, M, Goemans, N, De Luca, A, Pereda, A, Hemmings, R, Campion, G, Kaye, E, Arechavala-Gomeza, V, Goyenvalle, A, Niks, E, Veldhuizen, O, Furlong, P, Stoyanova-Beninska, V, Wood, M, Johnson, A, Mercuri, E, Muntoni, F, Sepodes, B, Haas, M, Vroom, E, Aartsma-Rus, A

Baskı/Yayın Bilgisi 2016

Journal article

Engineering exon-skipping vectors expressing U7 snRNA constructs for Duchenne muscular dystrophy gene therapy. Yazar: Goyenvalle, A, Davies, K

Challenges to oligonucleotides-based therapeutics for Duchenne muscular dystrophy. Yazar: Goyenvalle, A, Davies, K

Therapeutic approaches to muscular dystrophy. Yazar: Goyenvalle, A, Seto, J, Davies, K, Chamberlain, J

AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Babbs, A, Garcia, L, Davies, K

Upgrading U7snRNA To Complete Efficient Rescue of Dystrophin by Exon-Skipping in DMD Patients Yazar: Goyenvalle, A, Babbs, A, Garcia, L, Davies, K

AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Babbs, A, Wright, J, Garcia, L, Davies, K

Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy. Yazar: Goyenvalle, A, Babbs, A, van Ommen, G, Garcia, L, Davies, K

The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery. Yazar: Eckenfelder, A, Tordo, J, Babbs, A, Davies, K, Goyenvalle, A, Danos, O

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy Yazar: Goyenvalle, A, Wright, J, Babbs, A, Wilkins, V, Garcia, L, Davies, K

Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping. Yazar: Goyenvalle, A, Babbs, A, Powell, D, Kole, R, Fletcher, S, Wilton, S, Davies, K

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy. Yazar: Goyenvalle, A, Wright, J, Babbs, A, Wilkins, V, Garcia, L, Davies, K

Rescu of severely affected dystrophin/utrophin deficient mice by morpholino-oligomer mediated exon skipping Yazar: Goyenvalle, A, Babbs, A, Powell, D, Kole, R, Fletcher, S, Wilton, S, Davies, K

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping Yazar: Goyenvalle, A, Babbs, A, Wright, J, Wilkins, V, Powell, D, Garcia, L, Davies, K

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping. Yazar: Goyenvalle, A, Babbs, A, Wright, J, Wilkins, V, Powell, D, Garcia, L, Davies, K

AAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy Yazar: Le Hir, M, Goyenvalle, A, Peccate, C, Précigout, G, Davies, K, Voit, T, Garcia, L, Lorain, S

Tricyclo-DNA: A promising chemistry for the synthesis of antisense molecules for splice-switching approaches in DMD Yazar: Goyenvalle, A, Babbs, A, Avril, A, Griffiths, G, Dugovic, B, Davies, K, Leumann, C, Garcia, L

Diaphragm rescue alone prevents heart dysfunction in dystrophic mice. Yazar: Crisp, A, Yin, H, Goyenvalle, A, Betts, C, Moulton, H, Seow, Y, Babbs, A, Merritt, T, Saleh, A, Gait, M, Stuckey, D, Clarke, K, Davies, K, Wood, M

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