Showing 1 - 10 results of 10 for search 'H Al-Samkari', query time: 0.04s
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P1522: LONG-TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA by K. H. M. Kuo, D. M. Layton, A. Lal, H. Al-Samkari, J. Bhatia, P. A. Kosinski, B. Tong, M. Lynch, K. Uhlig, E. P. Vichinsky
Published 2022-06-01
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P1735: IMPROVEMENTS IN PATIENT-REPORTED OUTCOMES IN MITAPIVAT-TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL by K. H. Kuo, R. F. Grace, E. J. van Beers, W. Barcellini, A. Glenthøj, S. Holzhauer, P. Patel, V. Beynon, J. Li, E. Zagadailov, H. Al-Samkari
Published 2022-06-01
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P112: ENERGIZE AND ENERGIZE-T: TWO PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON--TRANSFUSION-DEPENDENT OR TRANSFUSION-DEPENDENT ALP... by K Kuo, D Layton, H Al-Samkari, A Kattamis, S Sheth, A Taher, V Viprakasit, C Chamberlain, L Czapla, S Gheuens, M Lynch, B Tong, K Uhlig, M Cappellini
Published 2022-01-01
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ENERGIZE AND ENERGIZE-T: TWO PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT OR TRANSFUSION-DEPENDENT ALPHA- OR... by KH Kuo, DM Layton, H Al-Samkari, A Kattamis, S Sheth, A Taher, V Viprakasit, CX Chamberlain, L Czapla, S Gheuens, L Jiang, M Lynch, B Tong, K Uhlig, MD Cappellini
Published 2021-10-01
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P1565: MITAPIVAT IMPROVES INEFFECTIVE ERYTHROPOIESIS AND REDUCES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by E. J. van Beers, H. Al-Samkari, R. F. Grace, W. Barcellini, A. Glenthøj, M. P. Judge, P. A. Kosinski, R. Xu, V. Beynon, B. McGee, J. B. Porter, K. H. M. Kuo
Published 2022-06-01
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P1548: LONG-TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY by W. Barcellini, R. F. Grace, H. Al-Samkari, A. Glenthøj, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, M. DiBacco, P. Hawkins, M. P. Judge, F. Tai, J. Morales-Arias, V. Beynon, E. J. van Beers
Published 2022-06-01
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P1544: BONE MINERAL DENSITY REMAINS STABLE IN PYRUVATE KINASE DEFICIENCY PATIENTS RECEIVING LONG-TERM TREATMENT WITH MITAPIVAT by H. Al-Samkari, R. F. Grace, A. Glenthøj, O. Andres, W. Barcellini, F. Galactéros, K. H. M. Kuo, D. M. Layton, M. Morado Arias, V. Viprakasit, Y. Dong, F. Tai, L. Grekas, K. Khoja, S. Gheuens, B. McGee, J. B. Porter, E. J. van Beers
Published 2022-06-01
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P1545: DURABILITY OF HEMOGLOBIN RESPONSE AND REDUCTION IN TRANSFUSION BURDEN IS MAINTAINED OVER TIME IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY TREATED WITH MITAPIVAT IN A LONG-TE... by R. F. Grace, A. Glenthøj, W. Barcellini, M. Verhovsek, J. A. Rothman, M. Morado Arias, D. M. Layton, O. Andres, F. Galactéros, E. J. van Beers, K. Onodera, V. Viprakasit, S. Chonat, J. B. Porter, M. P. Judge, P. A. Kosinski, P. Hawkins, S. Gheuens, R. Xu, B. McGee, V. Beynon, H. Al-Samkari
Published 2022-06-01
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