Clinical features and predictors for disease natural progression in adults with Pompe disease: a nationwide prospective observational study by van der Beek Nadine AME, de Vries Juna M, Hagemans Marloes LC, Hop Wim CJ, Kroos Marian A, Wokke John HJ, de Visser Marianne, van Engelen Baziel GM, Kuks Jan BM, van der Kooi Anneke J, Notermans Nicolette C, Faber Karin G, Verschuuren Jan JGM, Reuser Arnold JJ, van der Ploeg Ans T, van Doorn Pieter A

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