Allele-Specific Gene Editing Rescues Pathology in a Human Model of Charcot-Marie-Tooth Disease Type 2E by Carissa M. Feliciano, Carissa M. Feliciano, Kenneth Wu, Hannah L. Watry, Chiara B. E. Marley, Chiara B. E. Marley, Gokul N. Ramadoss, Gokul N. Ramadoss, Hana Y. Ghanim, Angela Z. Liu, Angela Z. Liu, Lyandysha V. Zholudeva, Todd C. McDevitt, Todd C. McDevitt, Mario A. Saporta, Bruce R. Conklin, Bruce R. Conklin, Bruce R. Conklin, Bruce R. Conklin, Luke M. Judge, Luke M. Judge

Get full text