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Editorial: Using Small Molecules to Treat Macromolecule Storage Disorders by Or Kakhlon, Pablo V. Escriba, Hasan O. Akman, Miguel Weil
Published 2020-11-01
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Bioavailability and cytosolic kinases modulate response to deoxynucleoside therapy in TK2 deficiencyResearch in context by Carlos Lopez-Gomez, Henly Hewan, Carlos Sierra, Hasan O. Akman, Maria J. Sanchez-Quintero, Marti Juanola-Falgarona, Saba Tadesse, Kurenai Tanji, Elisa E. Konofagou, Michio Hirano
Published 2019-08-01
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