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Anifrolumab Study for Treatment Effectiveness in the Real World (ASTER) among patients with systemic lupus erythematosus: protocol for an international observational effectiveness... by Marta Mosca, Stephanie Chen, Heide Stirnadel-Farrant, Cathy Emmas, Lucy Carty, Caroline Seo, Alessandro Sorrentino, Cassandra Nekeman-Nan, Samuel Chen, Miina Waratani
Published 2024-11-01
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Gene therapy in rare diseases: the benefits and challenges of developing a patient-centric registry for Strimvelis in ADA-SCID by Heide Stirnadel-Farrant, Mahesh Kudari, Nadia Garman, Jessica Imrie, Bikramjit Chopra, Stefania Giannelli, Michela Gabaldo, Ambra Corti, Stefano Zancan, Alessandro Aiuti, Maria Pia Cicalese, Rohit Batta, Jonathan Appleby, Mario Davinelli, Pauline Ng
Published 2018-04-01
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