α-L-iduronidase therapy for mucopolysaccharidosis type I by Jakub Tolar, Paul J Orchard

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Granulocyte colony-stimulating factor mobilized CFU-F can be found in the peripheral blood but have limited expansion potential by Troy C. Lund, Jakub Tolar, Paul J. Orchard

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372 HMGB1 Localization as a Driver of Carcinogenesis in RDEB-Associated Squamous Cell Carcinoma by Kacey Guenther Bui, Anja Bielinsky, Hai Dang Nguyen, Jakub Tolar

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Analysis of readability of the top web searches for pediatric inborn errors of fatty acid metabolism by Katelyn Sawyer, William Miller, Courtney Popp, Chloe Strege, Cindy Eide, Jakub Tolar

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Revertant Mosaicism in Epidermolysis Bullosa by Cameron Meyer-Mueller, Mark J. Osborn, Jakub Tolar, Christina Boull, Christen L. Ebens

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Impaired Mitochondrial and Metabolic Function of Fibroblasts Derived from Patients with Recessive Dystrophic and Junctional Epidermolysis Bullosa by Ilona Tietzová, Kirk Twaroski, Cindy Eide, Julie H. Ostrander, Peter A. Crawford, Jakub Tolar

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Modeling and rescue of defective blood–brain barrier function of induced brain microvascular endothelial cells from childhood cerebral adrenoleukodystrophy patients by Catherine A. A. Lee, Hannah S. Seo, Anibal G. Armien, Frank S. Bates, Jakub Tolar, Samira M. Azarin

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TP53 Modulates Oxidative Stress in Gata1+ Erythroid Cells by Ashley C. Kramer, Jenna Weber, Ying Zhang, Jakub Tolar, Ying Y. Gibbens, Margaret Shevik, Troy C. Lund

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Genome-wide Specificity of Highly Efficient TALENs and CRISPR/Cas9 for T Cell Receptor Modification by Friederike Knipping, Mark J. Osborn, Karl Petri, Jakub Tolar, Hanno Glimm, Christof von Kalle, Manfred Schmidt, Richard Gabriel

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Elevated cerebral spinal fluid cytokine levels in boys with cerebral adrenoleukodystrophy correlates with MRI severity. by Troy C Lund, Paul S Stadem, Angela Panoskaltsis-Mortari, Gerald Raymond, Weston P Miller, Jakub Tolar, Paul J Orchard

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A multitask clustering approach for single-cell RNA-seq analysis in Recessive Dystrophic Epidermolysis Bullosa. by Huanan Zhang, Catherine A A Lee, Zhuliu Li, John R Garbe, Cindy R Eide, Raphael Petegrosso, Rui Kuang, Jakub Tolar

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Bone marrow stromal and vascular smooth muscle cells have chemosensory capacity via bitter taste receptor expression. by Troy C Lund, Amanda J Kobs, Ashley Kramer, Mick Nyquist, Marcos T Kuroki, John Osborn, Diane S Lidke, Shalini T Low-Nam, Bruce R Blazar, Jakub Tolar

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MSC therapy attenuates obliterative bronchiolitis after murine bone marrow transplant. by Kashif Raza, Trevor Larsen, Nath Samaratunga, Andrew P Price, Carolyn Meyer, Amy Matson, Michael J Ehrhardt, Samuel Fogas, Jakub Tolar, Marshall I Hertz, Angela Panoskaltsis-Mortari

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CRISPR/Cas9-Based Lateral Flow and Fluorescence Diagnostics by Mark J. Osborn, Akshay Bhardwaj, Samuel P. Bingea, Friederike Knipping, Colby J. Feser, Christopher J. Lees, Daniel P. Collins, Clifford J. Steer, Bruce R. Blazar, Jakub Tolar

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Accumulation of senescence observed in spinocerebellar ataxia type 7 mouse model. by William Miller, Charles Lewis Humphrey Pruett, William Stone, Cindy Eide, Megan Riddle, Courtney Popp, Matthew Yousefzadeh, Christopher Lees, Davis Seelig, Elizabeth Thompson, Harry Orr, Laura Niedernhofer, Jakub Tolar

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Rapid DNA replication origin licensing protects stem cell pluripotency by Jacob Peter Matson, Raluca Dumitru, Philip Coryell, Ryan M Baxley, Weili Chen, Kirk Twaroski, Beau R Webber, Jakub Tolar, Anja-Katrin Bielinsky, Jeremy E Purvis, Jeanette Gowen Cook

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Correction: Rapid DNA replication origin licensing protects stem cell pluripotency by Jacob Peter Matson, Raluca Dumitru, Philip Coryell, Ryan M Baxley, Weili Chen, Kirk Twaroski, Beau R Webber, Jakub Tolar, Anja-Katrin Bielinsky, Jeremy E Purvis, Jeanette Gowen Cook

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Creation and characterization of novel rat model for recessive dystrophic epidermolysis bullosa: Frameshift mutation of the Col7a1 gene leads to severe blistered phenotype. by William Stone, Chloe Strege, William Miller, Aron M Geurts, Michael Grzybowski, Megan Riddle, Christopher Lees, Cindy Eide, Douglas R Keene, Sara F Tufa, Davis Seelig, John McGrath, Jakub Tolar

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PAX7 Targets, CD54, Integrin α9β1, and SDC2, Allow Isolation of Human ESC/iPSC-Derived Myogenic Progenitors by Alessandro Magli, Tania Incitti, James Kiley, Scott A. Swanson, Radbod Darabi, Fabrizio Rinaldi, Sridhar Selvaraj, Ami Yamamoto, Jakub Tolar, Ce Yuan, Ron Stewart, James A. Thomson, Rita C.R. Perlingeiro

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P63 targeted deletion under the FOXN1 promoter disrupts pre-and post-natal thymus development, function and maintenance as well as induces severe hair loss by Heather E. Stefanski, Yan Xing, Jemma Nicholls, Leslie Jonart, Emily Goren, Patricia A. Taylor, Alea A. Mills, Megan Riddle, John McGrath, Jakub Tolar, Georg A. Hollander, Bruce R. Blazar

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