Immunity and AAV-mediated gene therapy for muscular dystrophies in large animal models and human trials by Zejing eWang, Stephen J Tapscott, Stephen J Tapscott, Jeffrey S Chamberlain, Jeffrey S Chamberlain, Rainer eStorb, Rainer eStorb

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Microutrophin expression in dystrophic mice displays myofiber type differences in therapeutic effects. by Glen B Banks, Jeffrey S Chamberlain, Guy L Odom

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Functional deficits in nNOSmu-deficient skeletal muscle: myopathy in nNOS knockout mice. by Justin M Percival, Kendra N E Anderson, Paul Gregorevic, Jeffrey S Chamberlain, Stanley C Froehner

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Correction to: Expressing a Z-disk nebulin fragment innebulin-deficient mouse muscle: effects on muscle structure and function by Frank Li, Justin Kolb, Julie Crudele, Paola Tonino, Zaynab Hourani, John E. Smith, Jeffrey S. Chamberlain, Henk Granzier

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Muscle fiber type-predominant promoter activity in lentiviral-mediated transgenic mouse. by Tomohiro Suga, En Kimura, Yuka Morioka, Masahito Ikawa, Sheng Li, Katsuhisa Uchino, Yuji Uchida, Satoshi Yamashita, Yasushi Maeda, Jeffrey S Chamberlain, Makoto Uchino

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Biomarkers for Duchenne muscular dystrophy progression: impact of age in the mdx tongue spared muscle by Marcelo dos Santos Voltani Lorena, Estela Kato dos Santos, Renato Ferretti, G. A. Nagana Gowda, Guy L. Odom, Jeffrey S. Chamberlain, Cintia Yuri Matsumura

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Efficacy and muscle safety assessment of fukutin-related protein gene therapy by Halli Benasutti, Joseph W. Maricelli, Jane Seto, John Hall, Christine Halbert, Jacqueline Wicki, Lydia Heusgen, Nicholas Purvis, Michael Regnier, David C. Lin, Buel D. Rodgers, Jeffrey S. Chamberlain

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Innate and adaptive AAV-mediated immune responses in a mouse model of Duchenne muscular dystrophy by Michael R. Emami, Alejandro Espinoza, Courtney S. Young, Feiyang Ma, Philip K. Farahat, Philip L. Felgner, Jeffrey S. Chamberlain, Xiangmin Xu, April D. Pyle, Matteo Pellegrini, S. Armando Villalta, Melissa J. Spencer

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A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy by Chady H. Hakim, Nalinda B. Wasala, Xiufang Pan, Kasun Kodippili, Yongping Yue, Keqing Zhang, Gang Yao, Brittney Haffner, Sean X. Duan, Julian Ramos, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Dongsheng Duan

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