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Predicted deleterious variants in the human genome relevant to gene therapy with adeno-associated virus vectors by Mahboubeh R. Rostami, Philip L. Leopold, Jenifer M. Vasquez, Miguel de Mulder Rougvie, Alya Al Shakaki, Ali Ait Hssain, Amal Robay, Neil R. Hackett, Jason G. Mezey, Ronald G. Crystal
Published 2023-12-01
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