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Systemic gene therapy using an AAV44.9 vector rescues a neonatal lethal mouse model of propionic acidemia by Randy J. Chandler, Giovanni Di Pasquale, Eun-Young Choi, David Chang, Stephanie N. Smith, Jennifer L. Sloan, Victoria Hoffmann, Lina Li, John A. Chiorini, Charles P. Venditti
Published 2023-09-01
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