In vivo adenine base editing corrects newborn murine model of Hurler syndrome by Jing Su, Xiu Jin, Kaiqin She, Yi Liu, Li Song, Qinyu Zhao, Jianlu Xiao, Ruiting Li, Hongxin Deng, Fang Lu, Yang Yang

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In vivo base editing rescues photoreceptors in a mouse model of retinitis pigmentosa by Jing Su, Kaiqin She, Li Song, Xiu Jin, Ruiting Li, Qinyu Zhao, Jianlu Xiao, Danian Chen, Hui Cheng, Fang Lu, Yuquan Wei, Yang Yang

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Liver-directed gene therapy corrects neurologic disease in a murine model of mucopolysaccharidosis type I-Hurler by Xiu Jin, Jing Su, Qinyu Zhao, Ruiting Li, Jianlu Xiao, Xiaomei Zhong, Li Song, Yi Liu, Kaiqin She, Hongxin Deng, Yuquan Wei, Yang Yang

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Dual-AAV split prime editor corrects the mutation and phenotype in mice with inherited retinal degeneration by Kaiqin She, Yi Liu, Qinyu Zhao, Xiu Jin, Yiliu Yang, Jing Su, Ruiting Li, Li Song, Jianlu Xiao, Shaohua Yao, Fang Lu, Yuquan Wei, Yang Yang

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Delivery of nVEGFi using AAV8 for the treatment of neovascular age-related macular degeneration by Kaiqin She, Jing Su, Qingnan Wang, Yi Liu, Xiaomei Zhong, Xiu Jin, Qinyu Zhao, Jianlu Xiao, Ruiting Li, Hongxin Deng, Fang Lu, Yang Yang, Yuquan Wei

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