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The Charlotte Project: Recommendations for patient-reported outcomes and clinical parameters in Dravet syndrome through a qualitative and Delphi consensus study by Ángel Aledo-Serrano, Ana Mingorance, Vicente Villanueva, Juan José García-Peñas, Antonio Gil-Nagel, Susana Boronat, JoséÁngel Aibar, Silvia Cámara, María José Yániz, Luis Miguel Aras, Bárbara Blanco, Rocío Sánchez-Carpintero
Published 2022-09-01
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Heat-induced seizures, premature mortality, and hyperactivity in a novel Scn1a nonsense model for Dravet syndrome by Anat Mavashov, Anat Mavashov, Marina Brusel, Marina Brusel, Jiaxing Liu, Victoria Woytowicz, Haneui Bae, Ying-Hsin Chen, Vardhan S. Dani, Elena Cardenal-Muñoz, Vittoria Spinosa, José Ángel Aibar, Moran Rubinstein, Moran Rubinstein, Moran Rubinstein
Published 2023-05-01
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