Spinal Muscular Atrophy Treatment in Patients Identified by Newborn Screening—A Systematic Review by Karolina Aragon-Gawinska, Charlotte Mouraux, Tamara Dangouloff, Laurent Servais

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Response of plasma microRNAs to nusinersen treatment in patients with SMA by Irina T. Zaharieva, Mariacristina Scoto, Karolina Aragon‐Gawinska, Deborah Ridout, Bruno Doreste, Laurent Servais, Francesco Muntoni, Haiyan Zhou

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Long-term nusinersen treatment across a wide spectrum of spinal muscular atrophy severity: a real-world experience by Anna Łusakowska, Adrianna Wójcik, Anna Frączek, Karolina Aragon-Gawińska, Anna Potulska-Chromik, Paweł Baranowski, Ryszard Nowak, Grzegorz Rosiak, Krzysztof Milczarek, Dariusz Konecki, Zuzanna Gierlak-Wójcicka, Małgorzata Burlewicz, Anna Kostera-Pruszczyk

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