THromboprophylaxis In Sickle Cell Disease with central venous catheters (THIS): an internal pilot randomised controlled trial protocol by George Tomlinson, Ziad Solh, Jameel Abdulrehman, Kevin H M Kuo, Stephanie Forté, Lauren Bolster, Haowei (Linda) Sun, Pablo Bartolucci

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Untreated Anemia in Nontransfusion-dependent β-thalassemia: Time to Sound the Alarm by Khaled M. Musallam, Ali T. Taher, Maria Domenica Cappellini, Olivier Hermine, Kevin H. M. Kuo, Sujit Sheth, Vip Viprakasit, John B. Porter

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The variable manifestations of disease in pyruvate kinase deficiency and their management by Hanny Al-Samkari, Eduard J. van Beers, Kevin H.M. Kuo, Wilma Barcellini, Paola Bianchi, Andreas Glenthøj, María del Mar Mañú Pereira, Richard van Wijk, Bertil Glader, Rachael F. Grace

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P1497: MITAPIVAT IMPROVES IRON OVERLOAD IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE REGULARLY TRANSFUSED by Eduard van Beers, Hanny Al-Samkari, Rachael F. Grace, Wilma Barcellini, Andreas Glenthøj, Vanessa Beynon, Megan Wind-Rotolo, Rengyi Xu, Melissa Dibacco, Parija Patel, John B. Porter, Kevin H.M. Kuo

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P1466: EFFECT OF LUSPATERCEPT ON BONE MINERAL DENSITY IN PATIENTS WITH BETA‑THALASSEMIA ENROLLED IN THE PHASE 3 BELIEVE TRIAL by Thomas D. Coates, Maria Domenica Cappellini, Sujit Sheth, Kevin H.M. Kuo, Antonio Giulio Piga, Antonis Kattamis, Martina Perin, Frederik Lersch, Jeevan K. Shetty, Yinzhi Lai, Wen-Ling Kuo, Ali T. Taher

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P1479: COMORBIDITIES AND COMPLICATIONS IN ADULTS WITH PYRUVATE KINASE DEFICIENCY ACCORDING TO HEMOGLOBIN STRATA – A DESCRIPTIVE ANALYSIS FROM THE PEAK REGISTRY by Dagmar Pospíŝilová, Rachael F. Grace, Andreas Glenthøj, Carl Lander, Eduard van Beers, Bertil Glader, Mark Layton, Kevin H.M. Kuo, Juan-Luis Vives-Corrons, Yan Yan, Bryan Mcgee, Sara Higa, Paola Bianchi

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Designing a single-arm phase 2 clinical trial of mitapivat for adult patients with erythrocyte membranopathies (SATISFY): a framework for interventional trials in rare anaemias – p... by Niels Vejlstrup, Pierre Fenaux, Jesper Petersen, Eduard J van Beers, Andreas Glenthøj, Kevin H M Kuo, Richard van Wijk, Minke A E Rab, Evelyn Groot, Nina Toft, Selma Kofoed Bendtsen, Jens Helby, Fatiha Chermat

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Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatment by Hanny Al-Samkari, Rachael F. Grace, Andreas Glenthøj, Oliver Andres, Wilma Barcellini, Frédéric Galacteros, Kevin H. M. Kuo, D. Mark Layton, Marta Morado, Vip Viprakasit, Feng Tai, Rolandas Urbstonaitis, Jaime Morales, Bryan McGee, Eduard J. van Beers

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