A Comparative Analysis of Pricing and Reimbursement of Cystic Fibrosis Transmembrane Conductance Regulator Modulators in Europe by Khadidja Abdallah, Kris De Boeck, Marc Dooms, Steven Simoens

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Assays of CFTR Function In Vitro, Ex Vivo and In Vivo by Anabela Santo Ramalho, Mieke Boon, Marijke Proesmans, François Vermeulen, Marianne S. Carlon, Kris De Boeck

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Neutrophils from Patients with Primary Ciliary Dyskinesia Display Reduced Chemotaxis to CXCR2 Ligands by Maaike Cockx, Mieke Gouwy, Véronique Godding, Kris De Boeck, Jo Van Damme, Mieke Boon, Sofie Struyf

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The Effect of Synonymous Single-Nucleotide Polymorphisms on an Atypical Cystic Fibrosis Clinical Presentation by Giovana B. Bampi, Anabela S. Ramalho, Leonardo A. Santos, Johannes Wagner, Lieven Dupont, Harry Cuppens, Kris De Boeck, Zoya Ignatova

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Author Correction: Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing by Giulia Maule, Antonio Casini, Claudia Montagna, Anabela S. Ramalho, Kris De Boeck, Zeger Debyser, Marianne S. Carlon, Gianluca Petris, Anna Cereseto

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Long-Term Ivacaftor in People Aged 6 Years and Older with Cystic Fibrosis with Ivacaftor-Responsive Mutations by Joseph M. Pilewski, Kris De Boeck, Jerry A. Nick, Simon Tian, Cynthia DeSouza, Mark Higgins, Richard B. Moss

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Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing by Giulia Maule, Antonio Casini, Claudia Montagna, Anabela S. Ramalho, Kris De Boeck, Zeger Debyser, Marianne S. Carlon, Gianluca Petris, Anna Cereseto

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Phenotyping of Rare <i>CFTR</i> Mutations Reveals Distinct Trafficking and Functional Defects by Marjolein Ensinck, Liesbeth De Keersmaecker, Lise Heylen, Anabela S. Ramalho, Rik Gijsbers, Ricard Farré, Kris De Boeck, Frauke Christ, Zeger Debyser, Marianne S. Carlon

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Mucus Release and Airway Constriction by TMEM16A May Worsen Pathology in Inflammatory Lung Disease by Raquel Centeio, Jiraporn Ousingsawat, Inês Cabrita, Rainer Schreiber, Khaoula Talbi, Roberta Benedetto, Tereza Doušová, Eric K. Verbeken, Kris De Boeck, Isaac Cohen, Karl Kunzelmann

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Risk factors for forced expiratory volume in 1 s decline in European patients with cystic fibrosis: data from the European Cystic Fibrosis Society Patient Registry by Elpis Hatziagorou, Steffen Fieuws, Annalisa Orenti, Lutz Naehrlich, Uros Krivec, Meir Mei-Zahav, Andreas Jung, Kris De Boeck, on behalf of the ECFSPR Collaborative Group, Pfleger Andreas

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Optimisation of children z-score calculation based on new statistical techniques. by Antonio Martinez-Millana, Jessie M Hulst, Mieke Boon, Peter Witters, Carlos Fernandez-Llatas, Ines Asseiceira, Joaquin Calvo-Lerma, Ignacio Basagoiti, Vicente Traver, Kris De Boeck, Carmen Ribes-Koninckx

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G970R‐CFTR Mutation (c.2908G>C) Results Predominantly in a Splicing Defect by Meredith C. Fidler, Alexandra Buckley, James C. Sullivan, Marvin Statia, Sylvia F. Boj, Robert G. J. Vries, Anne Munck, Mark Higgins, Matteo Moretto Zita, Paul Negulescu, Fredrick vanGoor, Kris De Boeck

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Fifth Percentile Cutoff Values for Antipneumococcal Polysaccharide and Anti-Salmonella typhi Vi IgG Describe a Normal Polysaccharide Response by Heidi Schaballie, Barbara Bosch, Barbara Bosch, Rik Schrijvers, Marijke Proesmans, Kris De Boeck, Mieke Nelly Boon, François Vermeulen, Natalie Lorent, Doreen Dillaerts, Glynis Frans, Leen Moens, Inge Derdelinckx, Willy Peetermans, Bjørn Kantsø, Charlotte Svaerke Jørgensen, Marie-Paule Emonds, Xavier Bossuyt, Isabelle Meyts

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Change in Nutrient and Dietary Intake in European Children with Cystic Fibrosis after a 6-Month Intervention with a Self-Management mHealth Tool by Joaquim Calvo-Lerma, Mieke Boon, Jessie Hulst, Carla Colombo, Inês Asseiceira, María Garriga, Etna Masip, Ine Claes, Anna Bulfamante, Hettie M. Janssens, Maria Roca, Saioa Vicente, Victoria Fornés, Laura Zazzeron, Bo van Schijndel, Sandra Woodcock, Luisa Pereira, Kris de Boeck, Carmen Ribes-Koninckx

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Clinical validation of an evidence-based method to adjust Pancreatic Enzyme Replacement Therapy through a prospective interventional study in paediatric patients with Cystic Fibros... by Joaquim Calvo-Lerma, Jessie Hulst, Mieke Boon, Carla Colombo, Etna Masip, Mar Ruperto, Victoria Fornés-Ferrer, Els van der Wiel, Ine Claes, Maria Garriga, Maria Roca, Paula Crespo-Escobar, Anna Bulfamante, Sandra Woodcock, Sandra Martínez-Barona, Ana Andrés, Kris de Boeck, Carmen Ribes-Koninckx, MyCyFAPP project

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The effect of CFTR modulators on structural lung disease in cystic fibrosis by L. Clara Mok, L. Clara Mok, Antonio Garcia-Uceda, Antonio Garcia-Uceda, Matthew N. Cooper, Mariette Kemner-Van De Corput, Marleen De Bruijne, Marleen De Bruijne, Nathalie Feyaerts, Tim Rosenow, Tim Rosenow, Kris De Boeck, Stephen Stick, Stephen Stick, Stephen Stick, Harm A. W. M. Tiddens, Harm A. W. M. Tiddens

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Protocol for Application, Standardization and Validation of the Forskolin-Induced Swelling Assay in Cystic Fibrosis Human Colon Organoids by Annelotte M. Vonk, Peter van Mourik, Anabela S. Ramalho, Iris A.L. Silva, Marvin Statia, Evelien Kruisselbrink, Sylvia W.F. Suen, Johanna F. Dekkers, Frank P. Vleggaar, Roderick H.J. Houwen, Jasper Mullenders, Sylvia F. Boj, Robert Vries, Margarida D. Amaral, Kris de Boeck, Cornelis K. van der Ent, Jeffrey M. Beekman

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Assessing gastro-intestinal related quality of life in cystic fibrosis: Validation of PedsQL GI in children and their parents. by Mieke Boon, Ine Claes, Trudy Havermans, Victoria Fornés-Ferrer, Joaquim Calvo-Lerma, Inês Asseiceira, Anna Bulfamante, María Garriga, Etna Masip, Sandra Woodcock, Sylvia Walet, Celeste Barreto, Carla Colombo, Paula Crespo, Els Van der Wiel, Jessie Hulst, Sandra Martinez-Barona, Rita Nobili, Luisa Pereira, Mar Ruperto, Saioa Vicente, Kris De Boeck, Carmen Ribes-Koninckx, MyCyFAPP consortium

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