Carbidopa-based modulation of the functional effect of the AAV2-hAADC gene therapy in 6-OHDA lesioned rats. by Agnieszka Ciesielska, Nitasha Sharma, Janine Beyer, John Forsayeth, Krystof Bankiewicz

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Convection-enhanced delivery of AAV2-PrPshRNA in prion-infected mice. by Misol Ahn, Krystyna Bajsarowicz, Abby Oehler, Azucena Lemus, Krystof Bankiewicz, Stephen J DeArmond

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Efficacy of convection enhanced delivery of MTX110 (soluble panobinostat) in preclinical Diffuse Intrinsic Pontine Glioma models using metabolic hyperpolarized 13C imaging by Justyna M. Przystal, Ilwoo Park, Jie Zhang, Piotr Hadaczek, Krystof Bankiewicz, Nalin Gupta, Javad Nazarian, Sabine Mueller

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Gene Therapy in Movement Disorders: A Systematic Review of Ongoing and Completed Clinical Trials by Aristide Merola, Noelle Kobayashi, Alberto Romagnolo, Brenton A. Wright, Carlo Alberto Artusi, Gabriele Imbalzano, Irene Litvan, Amber D. Van Laar, Amber D. Van Laar, Krystof Bankiewicz

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Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe‐affected non‐human primates by intracerebral lentiviral gene therapy by Vasco Meneghini, Annalisa Lattanzi, Luigi Tiradani, Gabriele Bravo, Francesco Morena, Francesca Sanvito, Andrea Calabria, John Bringas, Jeanne M Fisher‐Perkins, Jason P Dufour, Kate C Baker, Claudio Doglioni, Eugenio Montini, Bruce A Bunnell, Krystof Bankiewicz, Sabata Martino, Luigi Naldini, Angela Gritti

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