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Phenotyping of Rare <i>CFTR</i> Mutations Reveals Distinct Trafficking and Functional Defects by Marjolein Ensinck, Liesbeth De Keersmaecker, Lise Heylen, Anabela S. Ramalho, Rik Gijsbers, Ricard Farré, Kris De Boeck, Frauke Christ, Zeger Debyser, Marianne S. Carlon
Published 2020-03-01
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Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids by Marjolein M. Ensinck, Liesbeth De Keersmaecker, Anabela S. Ramalho, Senne Cuyx, Stephanie Van Biervliet, Lieven Dupont, Frauke Christ, Zeger Debyser, François Vermeulen, Marianne S. Carlon
Published 2022-04-01
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