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A novel image-based high throughput screening assay discovers therapeutic candidates for adult polyglucosan body disease por Solmesky, L, Khazanov, N, Senderowitz, H, Wang, P, Minassian, B, Ferreira, I, Yue, W, Lossos, A, Weil, M, Kakhlon, O
Publicado em 2017Journal article -
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Guaiacol as a drug candidate for treating adult polyglucosan body disease por Kakhlon, O, Ferreira, I, Solmesky, L, Khazanov, N, Lossos, A, Alvarez, R, Yetil, D, Pampou, S, Weil, M, Senderowitz, H, Escriba, P, Yue, W, Akman, H
Publicado em 2018Journal article -
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Early clinical heterogeneity in choreoacanthocytosis. por Lossos, A, Dobson-Stone, C, Monaco, A, Soffer, D, Rahamim, E, Newman, J, Mohiddin, S, Fananapazir, L, Lerer, I, Linetsky, E, Reches, A, Argov, Z, Abramsky, O, Gadoth, N, Sadeh, M, Gomori, J, Boher, M, Meiner, V
Publicado em 2005Journal article