An S/MAR-based infectious episomal genomic DNA expression vector provides long-term regulated functional complementation of LDLR deficiency. за авторством Lufino, M, Manservigi, R, Wade-Martins, R

Advances in high-capacity extrachromosomal vector technology: episomal maintenance, vector delivery, and transgene expression. за авторством Lufino, M, Edser, P, Wade-Martins, R

An S/MAR-based infectious episomal genomic DNA expression vector provides long-term regulated functional complementation of LDLR deficiency за авторством Lufino, M, Manservigi, R, Wade-Martins, R

R-loops associated with triplet repeat expansions promote gene silencing in Friedreich ataxia and fragile X syndrome за авторством Groh, M, Lufino, M, Wade-Martins, R, Gromak, N

A Novel Genomic DNA-Reporter Gene Model for the Study of Friedreich's Ataxia in Neuronal Cells за авторством Lufino, M, Alegre-Abarrategui, J, Lim, F, Wade-Martins, R

The infectious BAC genomic DNA expression library: a high capacity vector system for functional genomics за авторством Lufino, M, Edser, P, Quail, M, Rice, S, Adams, D, Wade-Martins, R

Episomal transgene expression in pluripotent stem cells. за авторством Lufino, M, Popplestone, A, Cowley, S, Edser, P, James, W, Wade-Martins, R

A GAA repeat expansion reporter model of Friedreich's ataxia recapitulates the genomic context and allows rapid screening of therapeutic compounds. за авторством Lufino, M, Silva, A, Németh, A, Alegre-Abarrategui, J, Russell, A, Wade-Martins, R

Long-term physiologically regulated expression of the low-density lipoprotein receptor in vivo using genomic DNA mini-gene constructs. за авторством Hibbitt, O, McNeil, E, Lufino, M, Seymour, L, Channon, K, Wade-Martins, R

LRRK2 regulates autophagic activity and localizes to specific membrane microdomains in a novel human genomic reporter cellular model. за авторством Alegre-Abarrategui, J, Christian, H, Lufino, M, Mutihac, R, Venda, L, Ansorge, O, Wade-Martins, R