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Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR by Cehajic-Kapetanovic, J, Xue, K, Martinez-Fernandez de la Camara, C, Nanda, A, Davies, A, Wood, LJ, Salvetti, AP, Fischer, MD, Aylward, JW, Barnard, AR, Jolly, JK, Luo, E, Lujan, BJ, Ong, T, Girach, A, Black, GCM, Gregori, NZ, Davis, JL, Rosa, PR, Lotery, AJ, Lam, BL, Stanga, PE, MacLaren, RE
Published 2020Journal article