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P112: ENERGIZE AND ENERGIZE-T: TWO PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON--TRANSFUSION-DEPENDENT OR TRANSFUSION-DEPENDENT ALP... per K Kuo, D Layton, H Al-Samkari, A Kattamis, S Sheth, A Taher, V Viprakasit, C Chamberlain, L Czapla, S Gheuens, M Lynch, B Tong, K Uhlig, M Cappellini
Publicat 2022-01-01
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5612617 EFFICACY AND SAFETY OF A SINGLE DOSE OF EXAGAMGLOGENE AUTOTEMCEL FOR TRANSFUSION-DEPENDENT-THALASSEMIA AND SEVERE SICKLE CELL DISEASE per J. de la Fuente, F. Locatelli, H. Frangoul, S. Corbacioglu, D. Wall, M. Cappellini, M. de Montalembert, A. Kattamis, S. Lobitz, D. Rondelli, S. Sheth, M. Steinberg, M. Walters, Y. Bobruff, C. Simard, Y. Song, L. Zhang, A. Sharma, S. Imren, B. Hobbs, S. Grupp
Publicat 2023-04-01
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S106: LONG-TERM FOLLOW-UP OF BETA-THALASSEMIA PATIENTS TREATED WITH HEMATOPOIETIC STEM CELL GENE THERAPY per S Marktel, S Scaramuzza, F Giglio, M Cicalese, M Lidonnici, C Rossi, V Calbi, N Masera, E D’Angelo, N Mirra, R Origa, I Tartaglione, S Perrotta, G Viarengo, L Santoleri, R Milani, S Gattillo, A Calabria, E Montini, G Graziadei, L Naldini, M Cappellini, A Aiuti, F Ciceri, G Ferrari
Publicat 2022-01-01
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