AAV-vectored base editor trans-splicing delivers dystrophin repair by Zhen Li, Manuel A.F.V. Gonçalves

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DNA, RNA, and Protein Tools for Editing the Genetic Information in Human Cells by Xiaoyu Chen, Manuel A.F.V. Gonçalves

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Adenoviral Vectors Meet Gene Editing: A Rising Partnership for the Genomic Engineering of Human Stem Cells and Their Progeny by Francesca Tasca, Qian Wang, Manuel A.F.V. Gonçalves

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Novel Therapeutic Approaches for the Treatment of Retinal Degenerative Diseases: Focus on CRISPR/Cas-Based Gene Editing by Carmen Gallego, Manuel A. F. V. Gonçalves, Jan Wijnholds, Jan Wijnholds

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The Chromatin Structure Differentially Impacts High-Specificity CRISPR-Cas9 Nuclease Strategies by Xiaoyu Chen, Jin Liu, Josephine M. Janssen, Manuel A.F.V. Gonçalves

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The Chromatin Structure of CRISPR-Cas9 Target DNA Controls the Balance between Mutagenic and Homology-Directed Gene-Editing Events by Josephine M. Janssen, Xiaoyu Chen, Jin Liu, Manuel A.F.V. Gonçalves

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High-Capacity Adenoviral Vectors Permit Robust and Versatile Testing of <i>DMD</i> Gene Repair Tools and Strategies in Human Cells by Marcella Brescia, Josephine M. Janssen, Jin Liu, Manuel A. F. V. Gonçalves

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Rapid and sensitive lentivirus vector-based conditional gene expression assay to monitor and quantify cell fusion activity. by Manuel A F V Gonçalves, Josephine M Janssen, Maarten Holkers, Antoine A F de Vries

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High-capacity adenovector delivery of forced CRISPR-Cas9 heterodimers fosters precise chromosomal deletions in human cells by Francesca Tasca, Marcella Brescia, Jin Liu, Josephine M. Janssen, Kamel Mamchaoui, Manuel A.F.V. Gonçalves

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Targeted chromosomal insertion of large DNA into the human genome by a fiber-modified high-capacity adenovirus-based vector system. by Manuel A F V Gonçalves, Maarten Holkers, Gijsbert P van Nierop, Roeland Wieringa, Maria G Pau, Antoine A F de Vries

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In trans paired nicking triggers seamless genome editing without double-stranded DNA cutting by Xiaoyu Chen, Josephine M. Janssen, Jin Liu, Ignazio Maggio, Anke E. J. ‘t Jong, Harald M.M. Mikkers, Manuel A. F. V. Gonçalves

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A Small Key for a Heavy Door: Genetic Therapies for the Treatment of Hemoglobinopathies by Hidde A. Zittersteijn, Cornelis L. Harteveld, Stefanie Klaver-Flores, Arjan C. Lankester, Rob C. Hoeben, Frank J. T. Staal, Manuel A. F. V. Gonçalves

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Long-Term Contribution of Human Bone Marrow Mesenchymal Stromal Cells to Skeletal Muscle Regeneration in Mice by Anabel S. De La Garza-Rodea, Ietje Van Der Velde, Hester Boersma, Manuel A. F. V. Gonçalves, Dirk W. Van Bekkum, Antoine A. F. De Vries, Shoshan Knaän-Shanzer Ph.D.

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Myogenic Properties of Human Mesenchymal Stem Cells Derived from Three Different Sources by Anabel S. De La Garza-Rodea, Ietje Van Der Velde-Van Dijke, Hester Boersma, Manuel A. F. V. Gonçalves, Dirk W. Van Bekkum, Antoine A. F. De Vries, Shoshan Knaän-Shanzer Ph.D.

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Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi by Alessia Cavazza, Ayal Hendel, Rasmus O. Bak, Paula Rio, Marc Güell, Duško Lainšček, Virginia Arechavala-Gomeza, Ling Peng, Fatma Zehra Hapil, Joshua Harvey, Francisco G. Ortega, Coral Gonzalez-Martinez, Carsten W. Lederer, Kasper Mikkelsen, Giedrius Gasiunas, Nechama Kalter, Manuel A.F.V. Gonçalves, Julie Petersen, Alejandro Garanto, Lluis Montoliu, Marcello Maresca, Stefan E. Seemann, Jan Gorodkin, Loubna Mazini, Rosario Sanchez, Juan R. Rodriguez-Madoz, Noelia Maldonado-Pérez, Torella Laura, Michael Schmueck-Henneresse, Cristina Maccalli, Julian Grünewald, Gloria Carmona, Neli Kachamakova-Trojanowska, Annarita Miccio, Francisco Martin, Giandomenico Turchiano, Toni Cathomen, Yonglun Luo, Shengdar Q. Tsai, Karim Benabdellah

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