AAV-vectored base editor trans-splicing delivers dystrophin repair by Zhen Li, Manuel A.F.V. Gonçalves

Get full text

DNA, RNA, and Protein Tools for Editing the Genetic Information in Human Cells by Xiaoyu Chen, Manuel A.F.V. Gonçalves

Get full text

Adenoviral Vectors Meet Gene Editing: A Rising Partnership for the Genomic Engineering of Human Stem Cells and Their Progeny by Francesca Tasca, Qian Wang, Manuel A.F.V. Gonçalves

Get full text

Modular and excisable molecular switch for the induction of gene expression by the yeast FLP recombinase by Maarten Holkers, Antoine A.F. de Vries, Manuel A.F.V. Gonçalves

Get full text

The Chromatin Structure of CRISPR-Cas9 Target DNA Controls the Balance between Mutagenic and Homology-Directed Gene-Editing Events by Josephine M. Janssen, Xiaoyu Chen, Jin Liu, Manuel A.F.V. Gonçalves

Get full text

High-Capacity Adenoviral Vectors Permit Robust and Versatile Testing of <i>DMD</i> Gene Repair Tools and Strategies in Human Cells by Marcella Brescia, Josephine M. Janssen, Jin Liu, Manuel A. F. V. Gonçalves

Get full text

High-capacity adenovector delivery of forced CRISPR-Cas9 heterodimers fosters precise chromosomal deletions in human cells by Francesca Tasca, Marcella Brescia, Jin Liu, Josephine M. Janssen, Kamel Mamchaoui, Manuel A.F.V. Gonçalves

Get full text

Targeted chromosomal insertion of large DNA into the human genome by a fiber-modified high-capacity adenovirus-based vector system. by Manuel A F V Gonçalves, Maarten Holkers, Gijsbert P van Nierop, Roeland Wieringa, Maria G Pau, Antoine A F de Vries

Get full text

Myogenic Properties of Human Mesenchymal Stem Cells Derived from Three Different Sources by Anabel S. De La Garza-Rodea, Ietje Van Der Velde-Van Dijke, Hester Boersma, Manuel A. F. V. Gonçalves, Dirk W. Van Bekkum, Antoine A. F. De Vries, Shoshan Knaän-Shanzer Ph.D.

Get full text

Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group by Alessia Cavazza, Francisco J. Molina-Estévez, Álvaro Plaza Reyes, Victor Ronco, Asma Naseem, Špela Malenšek, Peter Pečan, Annalisa Santini, Paula Heredia, Araceli Aguilar-González, Houria Boulaiz, Qianqian Ni, Marina Cortijo-Gutierrez, Kristina Pavlovic, Inmaculada Herrera, Berta de la Cerda, Emilio M. Garcia-Tenorio, Eva Richard, Sergio Granados-Principal, Arístides López-Márquez, Mariana Köber, Marijana Stojanovic, Melita Vidaković, Irene Santos-Garcia, Lorea Blázquez, Emily Haughton, Dongnan Yan, Rosario María Sánchez-Martín, Loubna Mazini, Gloria Gonzalez Aseguinolaza, Annarita Miccio, Paula Rio, Lourdes R. Desviat, Manuel A.F.V. Gonçalves, Ling Peng, Cecilia Jiménez-Mallebrera, Francisco Martin Molina, Dhanu Gupta, Duško Lainšček, Yonglun Luo, Karim Benabdellah

Get full text

Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi by Alessia Cavazza, Ayal Hendel, Rasmus O. Bak, Paula Rio, Marc Güell, Duško Lainšček, Virginia Arechavala-Gomeza, Ling Peng, Fatma Zehra Hapil, Joshua Harvey, Francisco G. Ortega, Coral Gonzalez-Martinez, Carsten W. Lederer, Kasper Mikkelsen, Giedrius Gasiunas, Nechama Kalter, Manuel A.F.V. Gonçalves, Julie Petersen, Alejandro Garanto, Lluis Montoliu, Marcello Maresca, Stefan E. Seemann, Jan Gorodkin, Loubna Mazini, Rosario Sanchez, Juan R. Rodriguez-Madoz, Noelia Maldonado-Pérez, Torella Laura, Michael Schmueck-Henneresse, Cristina Maccalli, Julian Grünewald, Gloria Carmona, Neli Kachamakova-Trojanowska, Annarita Miccio, Francisco Martin, Giandomenico Turchiano, Toni Cathomen, Yonglun Luo, Shengdar Q. Tsai, Karim Benabdellah

Get full text