Showing 1 - 13 results of 13 for search 'Manzano, R', query time: 0.73s
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Enantioselective silver and amine co-catalyzed desymmetrizing cycloisomerization of alkyne-linked cyclohexanones by Manzano, R, Datta, S, Paton, RS, Dixon, DJ
Published 2017Journal article -
2
Enantioselective silver-catalyzed cascade synthesis of fused lactone and lactam oxazolines by De La Campa, R, Manzano, R, Calleja, P, Ellis, SR, Dixon, DJ
Published 2018Journal article -
3
Development of LNA gapmer oligonucleotide-based therapy for ALS/FTD caused by the C9orf72 repeat expansion by Sathyaprakash, C, Manzano, R, Varela, MA, Hashimoto, Y, Wood, MJA, Talbot, K, Aoki, Y
Published 2020Journal article -
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Dual catalytic enantioselective desymmetrization of allene-tethered cyclohexanones by Zhang, L, Yamazaki, K, Leitch, JA, Manzano, R, Atkinson, AM, Hamlin, TA, Dixon, DJ
Published 2020Journal article -
5
Beyond motor neurons: expanding the clinical spectrum in Kennedy’s disease by Manzano, R, Sorarú, G, Grunseich, C, Fratta, P, Zuccaro, E, Pennuto, M, Rinaldi, C
Published 2018Journal article -
6
Alpha-synuclein induces the unfolded protein response in Parkinson's disease SNCA triplication iPSC-derived neurons by Heman-Ackah, S, Manzano, R, Hoozemans, J, Scheper, W, Flynn, R, Haerty, W, Cowley, S, Bassett, A, Wood, M
Published 2017Journal article -
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Peptide-conjugated phosphodiamidate oligomer-mediated exon skipping has benefits for cardiac function in mdx and Cmah-/-mdx mouse models of Duchenne muscular dystrophy by Blain, A, Greally, E, McClorey, G, Manzano, R, Betts, C, Godfrey, C, O'Donovan, L, Coursindel, T, Gait, M, Wood, M, Macgowan, G, Straub, V
Published 2018Journal article -
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Cmah-dystrophin deficient mdx mice display an accelerated cardiac phenotype that is improved following peptide-PMO exon skipping treatment by Betts, C, McClorey, G, Healicon, R, Hammond, S, Manzano, R, Muses, S, Ball, V, Godfrey, C, Merritt, T, van Westering, T, O'Donovan, L, Wells, K, Gait, M, Wells, D, Tyler, D, Wood, M
Published 2018Journal article -
10
AR cooperates with SMAD4 to maintain skeletal muscle homeostasis by Forouhan, M, Lim, WF, Zanetti-Domingues, LC, Tynan, CJ, Roberts, TC, Malik, B, Manzano, R, Speciale, AA, Ellerington, R, Garcia-Guerra, A, Fratta, P, Sorarú, G, Greensmith, L, Pennuto, M, Wood, MJA, Rinaldi, C
Published 2022Journal article -
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C9orf72 and RAB7L1 regulate vesicle trafficking in amyotrophic lateral sclerosis and frontotemporal dementia by Aoki, Y, Manzano, R, Lee, Y, Dafinca, R, Aoki, M, Douglas, A, Varela, M, Sathyaprakash, C, Scaber, J, Barbagallo, P, Vader, P, Mäger, I, Ezzat, K, Turner, M, Ito, N, Gasco, S, Ohbayashi, N, El Andaloussi, S, Takeda, S, Fukuda, M, Talbot, K, Wood, M
Published 2017Journal article -
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C9ORF72 and RAB7L1 regulate vesicle trafficking in amyotrophic lateral sclerosis and frontotemporal dementia by Manzano, R, Aoki, Y, Lee, Y, Nca, RD, Aoki, M, Douglas, AGL, Varela, MA, Sathyaprakash, C, Scaber, J, Barbagallo, P, Vader, P, Mager, I, Ezzat, K, Turner, MR, Ito, N, Gasco, S, Ohbayashi, N, El Andaloussi, S, Taked, S, Fukuda, M, Talbot, K, Wood, MJA
Published 2017Conference item -
13
Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity by Lim, WF, Forouhan, M, Roberts, TC, Dabney, J, Ellerington, R, Speciale, AA, Manzano, R, Lieto, M, Sangha, G, Banerjee, S, Conceição, M, Cravo, L, Biscans, A, Roux, L, Pourshafie, N, Grunseich, C, Duguez, S, Khvorova, A, Pennuto, M, Cortes, CJ, La Spada, AR, Fischbeck, KH, Wood, MJA, Rinaldi, C
Published 2021Journal article