Identification of novel small molecule-based strategies of COL7A1 upregulation and readthrough activity for the treatment of recessive dystrophic epidermolysis bullosa by Irene Jover, Maria C. Ramos, María José Escámez, Estrella Lozoya, José R. Tormo, Diana de Prado-Verdún, Ángeles Mencía, Mercè Pont, Carles Puig, Marie-Helene Larraufie, Cristina Gutiérrez-Caballero, Fernando Reyes, Juan Luis Trincado, Vicente García-González, Rosario Cerrato, Miriam Andrés, Maribel Crespo, Francisca Vicente, Nuria Godessart, Olga Genilloud, Fernando Larcher, Arsenio Nueda

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