Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells by Patrick Bittorf, Thorsten Bergmann, Simone Merlin, Cristina Olgasi, Oliver Pullig, Ralf Sanzenbacher, Martin Zierau, Heike Walles, Antonia Follenzi, Joris Braspenning

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Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device by Cristina Olgasi, Chiara Borsotti, Simone Merlin, Thorsten Bergmann, Patrick Bittorf, Adeolu Badi Adewoye, Nicholas Wragg, Kelcey Patterson, Andrea Calabria, Fabrizio Benedicenti, Alessia Cucci, Alessandra Borchiellini, Berardino Pollio, Eugenio Montini, Delfina M. Mazzuca, Martin Zierau, Alexandra Stolzing, Philip.M. Toleikis, Joris Braspenning, Antonia Follenzi

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